UCSF Benioff Children's Hospital Oakland
Hematology/Oncology Department
UCSF Benioff Children's Hospital Oakland


Recent Faculty Publications (2014 - 2016)

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BOOKS BOOK CHAPTERS DATABASES JOURNAL ARTICLES EDITORIALS LETTERS ABSTRACTS INVITED LECTURES PRESENTATIONS

Books:

2016:

2015:

2014:


Book Chapters:

2016:

  • Long LS, Agrawal AK. Pediatrics. In: Gulati A, Puttanniah V, Byas-Smith M, eds. Essentials of Interventional Cancer Pain Management. New York: Springer; 2016 (in press).
  • Agrawal AK, Feusner J. Supportive Care of Patients with Cancer. In: Lanzkowsky P, Lipton JM, Fish JD, eds. Lanzkowsky's Manual of Pediatric Hematology and Oncology. 6th ed: Springer; 2016. http://www.amazon.com/Lanzkowskys-Manual-Pediatric-Hematology-Oncology/dp/0128013680.
  • Fung EB, Schroepher C, Lal A. Nutrition for Patients with Thalassemia. In: Watson RR, Mahadevan D, eds. Handbook of nutrition and diet in leukemia and blood disease therapy chapter 19: Wageningen Pers (February 5, 2016); 2016:315-34. http://www.amazon.com/Handbook-Nutrition-Leukemia-Disease-Handbooks/dp/9086862772.
  • Rai P, Vichinsky E. COMMENTARY on: "Controlled Trial of Transfusion for Silent Cerebral Infarcts in Sickle Cell Anemia". In: Cabana MD, Goldstein AM, De Gialluly PS, Schroeder A, eds. Year Book of Pediatrics 2016. Philadelphia, PA: Elsevier Mosby; 2016. http://store.elsevier.com/product.jsp?isbn=00843954.
  • Singer ST. Fertility Issues in Transfusion Dependent Thalassemia: Pathophysiology, Assessment and Management. In: Infertility in Adolescents and Young Adults. New York: Springer; 2016 (October).
  • Walters MC. Hematopoietic cell transplantation for sickle cell disease. In: Forman SJ, Negris RS, Antin J, Applebaum FR, eds. Hematopoietic Cell Transplantation. Fifth ed. (March 2016). Malden, MA: Blackwell Science; 2016. http://www.wiley.com/WileyCDA/WileyTitle/productCd-1118416120.html.
  • Winstead M, Vichinsky E. Sickle Cell Disease: Management of Complications. In: Non-Malignant Hematology: Expert Clinical Perspective. Springer; 2016 (in press).

2015:

2014:

  • Calloway CD, Erlich H. Evolving technologies in forensic DNA analysis. In: Primorac D, Schanfield M, eds. Forensic DNA Applications: an Interdisciplinary Perspective. Boca Raton, FL: CRC Press, Taylor and Francis; 2014:417-28.
  • Fung EB, Chung J. Nutrition for Children with Sickle Cell Disease and Thalassemia. In: Kleinman RE, Greer FR, eds. Pediatric Nutrition Handbook. 7th ed. Elk Grove Village, IL: American Academy of Pediatrics; 2014:979-92. http://reader.aappublications.org/pediatric-nutrition-7th-edition-sponsored-member-benefit/2.
  • Garcia JR, Walters MC. Hematopoietic cell transplantation for non-malignant disorders. In: Greer J, ed. Wintrobe's Clinical Hematology. 13th ed. Philadelphia, PA: Wolwers Kluwer/Lippincott Williams & Wilkins; 2014: .
  • Garcia A, Gallagher C, McClain E. Pediatric Apheresis: Special Considerations for Children < 25kg. In Linz, W ed. Principles of Apheresis Technology, Fifth ed. Vancouver,BC, American Society for Apheresis, 2014. https://asfamalachite-mgmt.site-ym.com/store/ViewProduct.aspx?id=2630448.
  • Lalefar NR, Lubin B. Sibling Donor Cord Blood Program: Children's Hospital Research Center Oakland and Beyond. In: Dusko I, ed. Stem Cell Banking. New York, NY: Humana Press/Springer Science; 2014. http://www.amazon.com/Stem-Banking-Biology-Regenerative-Medicine/dp/1493905848.

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Electronic Database Articles

2016:

  • DeBaun M, Vichinsky E. Red blood cell transfusion in sickle cell disease. In: Schrier SL, Mahoney DH, Tirnauer J, eds. UpToDate, Topic 90145: Version 17; May 26, 2016. UpToDate, Inc., Waltham, MA. Link.
  • DeBaun M, Vichinsky E. Vasoocclusive pain management in sickle cell disease. In: Mahoney DH, Schrier SL, Tirnauer J, eds. UpToDate, Topic 7144: Version 19; Apr 05, 2016. UpToDate, Inc., Waltham, MA. Link.
  • Field J, Vichinsky E, DeBaun M. Overview of the management and prognosis of sickle cell disease. In: Schrier SL, Mahoney DH, Tirnauer J, eds. UpToDate, Topic 7114: Version 45; May 25, 2016. UpToDate, Inc., Waltham, MD. Link.
  • Vichinsky E. Overview of the clinical manifestations of sickle cell disease. In: Schrier SL, Tirnauer J, eds. UpToDate, Topic 7119: Version 32; May 26, 2016. UpToDate, Inc., Waltham, MA. Link.
  • Vichinsky E. Overview of variant sickle cell syndromes. In: Mahoney DH, Tirnauer J, eds. UpToDate, Topic 7115: Version 13; March 18, 2016. UpToDate, Inc., Waltham, MA. Link.
  • Vichinsky E. Pregnancy in women with sickle cell disease. In: Schrier SL, Ramin SM, Tirnauer J, Barss V, eds. UpToDate. Topic 7139: Version 24; March 29, 2016. UpToDate, Inc., Waltham, MA. Link.

2015:

2014:

  • Agrawal A. Guidelines on the treatment of skin and oral HIV-associated conditions in children and adults. World Health Organization (WHO).
  • Anglemyer A, Agrawal AK, Rutherford GW. Treatment of Kaposi sarcoma in children with HIV-1 infection. Cochrane Database Syst Rev 2014;1:CD009826. http://www.ncbi.nlm.nih.gov/pubmed/24464843.
  • DeBaun M, Vichinsky E. Acute pain management in adults with sickle cell disease. In: Basow DS, ed. UpToDate. Topic 7144 Version 14.0; Oct, 2014. UpToDate, Inc., Waltham, MA. Link.
  • DeBaun M, Vichinsky E. Red blood cell transfusion in sickle cell disease. In: Basow DS, ed. UpToDate. Topic 90145 Version 8.0; Nov 11, 2014. UpToDate, Inc., Waltham, MA. Link.
  • Field J, Vichinsky E, DeBaun M. Overview of the management and prognosis of sickle cell disease. In: Basow DS, ed. UpToDate. Topic 7114 Version 37.0; Dec 01, 2014. UpToDate, Inc., Waltham, MA. Link.
  • Vichinsky E. Overview of the clinical manifestations of sickle cell disease. In: Basow DS, ed. UpToDate. Topic 7119 Version 27.0; Nov. 24, 2014. UpToDate, Inc., Waltham, MA. Link.
  • Vichinsky E. Pregnancy in women with sickle cell disease. In: Basow DS, ed. UpToDate. Topic 7139 Version 18.0; Sep 30, 2014. UpToDate, Inc., Waltham, MA. Link.
  • Vichinsky E. Sickle Cell Trait. In: Basow DS, ed. UpToDate. Topic 7145 Version 24.0; Nov 21 2014. UpToDate, Inc., Waltham, MA. Link.
  • Vichinsky E. Variant Sickle Cell Syndromes. In: Basow DS, ed. UpToDate. Topic 7115 Version 11.0; March 28, 2014. UpToDate, Inc., Waltham, MA.Link.
  • Vichinsky E, Mahoney DH. Diagnosis of sickle cell disorders. In: Basow DS, ed. UpToDate. Topic 7113 Version 15.0; Aug 28, 2014. UpToDate, Inc., Waltham, MA. Link.

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Journal Articles:

2016:

  • Abla O, Kutny M, Testi A, Feusner J. Management of relapsed and refractory acute promyelocytic leukemia: recommendations from an international expert panel. Blood 2016 (submitted).
  • Anie KA, Treadwell MJ, Grant AM, Dennis-Antwi JA, Asafo MK, Lamptey ME, Ojodu J, Yusuf C, Otaigbe A, Ohene-Frempong K. Community engagement to inform the development of a sickle cell counselor training and certification program in Ghana. J Community Genet 2016. http://www.ncbi.nlm.nih.gov/pubmed/27090687.
  • Block G, Epel E, Holland NT, Blackburn EH, Lin J, Jensen CD, Fung E, Hudes M. Telemere length: association with nutrition and body fat in a healthy non-smoking sample. Review PLOS One; January 2016.
  • Cabrales P, Scicinski J, Reid T, Kuypers F, Larkin S, Fens M, Oronsky A, Oronsky B. A look inside the mechanistic black box: Are red blood cells the critical effectors of RRx-001 cytotoxicity? Med Oncol 2016;33 7:63. http://www.ncbi.nlm.nih.gov/pubmed/27229330.
  • Chu J, Guo H, Raphael R, Torkildson J, Vichinsky E, Garrett C, Hastings C. Disseminated juvenile xanthogranuloma culminating in bone marrow necrosis and death. 2016 (submitted).
  • Chung J, Gildengorin G, Higa A, Fung EB. Zinc metabolism in newly diagnosed oncologic disorders. J Ped Hem Onc 2016 (in process).
  • Coombs CC, DeAngelis LM, Feusner JH, Rowe JM, Tallman MS. Pseudotumor Cerebri in Acute Promyelocytic Leukemia Patients on Intergroup Protocol 0129: Clinical Description and Recommendations for New Diagnostic Criteria. Clin Lymphoma Myeloma Leuk 2016;16 3:146-51. http://www.ncbi.nlm.nih.gov/pubmed/26724834.
  • DeWitt M, Magis W, Bray N, Wang T, Berman J, Urbinati F, Munoz D, Kohn D, Walters MC, Carroll D, Martin DK, Corn JE. Efficient Correction of the Sickle Mutation in Human Hematopoietic Stem Cells Using a Cas9 Ribonucleoprotein Complex BioRxIV 2016;dx.doi.org/10.1101/036236 Jan 15, 2016. Link.
  • Dix D, Aplenc R, Bowes L, Cellot S, Ethier MC, Feusner J, Gillmeister B, Johnston DL, Lewis V, Michon B, Mitchell D, Portwine C, Price V, Silva M, Stobart K, Yanofsky R, Zelcer S, Beyene J, Sung L. Impact of registration on clinical trials on infection risk in pediatric acute myeloid leukemia. Int J Cancer 2016;138 7:1785-91. http://www.ncbi.nlm.nih.gov/pubmed/26515793.
  • Dowling MM, Ramaciotti C, Kanter J, Osunkwo I, Inusa B, Lyer R, Kwiatkovvski J, Johnson C, Rhodes MM, Owen W, Strouse JJ, Quinn C, Panepinto JA, Neumayr L, Sarnaik S, Hynan LS, Plumb P, Kirkham F. Increased Prevalence of Potential Right-to-Left Shunting in Children with Sickle Cell Anemia and Stroke. Blood 2016 (submitted).
  • El-Mallawany NK, Kamiyango W, Villiera J, ... Agrawal A, et al. The Lilongwe pediatric Kaposi sarcoma staging classification: retrospective validation and prognostic significance in HIV-infected children and adolescents in Malawi. 2016 (submitted).
  • Fung EB. The importance of nutrition for health in patients with transfusion-dependent thalassemia. Ann N Y Acad Sci 2016;1368 1:40-8. http://www.ncbi.nlm.nih.gov/pubmed/26824448.
  • Heeney MM, Hoppe CC, Abboud MR, Inusa B, Kanter J, Ogutu B, Brown PB, Heath LE, Jakubowski JA, Zhou C, Zamoryakhin D, Agbenyega T, Colombatti R, Hassab HM, Nduba VN, Oyieko JN, Robitaille N, Segbefia CI, Rees DC, Dove Investigators. A Multinational Trial of Prasugrel for Sickle Cell Vaso-Occlusive Events. N Engl J Med 2016;374 7:625-35. http://www.ncbi.nlm.nih.gov/pubmed/26644172.
  • Heeney MM, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E. Comparison of clinical outcomes between adult and pediatric patients with sickle cell disease: 3-year follow-up in a prospective, longitudinal, noninterventional registry trial. 2016 (submitted)
  • Hoppe CC, Styles L, Heath LE, Zhou C, Jakubowski JA, Winters KJ, Brown PB, Rees DC, Heeney MM. Design of the DOVE (Determining Effects of Platelet Inhibition on Vaso-Occlusive Events) trial: A global Phase 3 double-blind, randomized, placebo-controlled, multicenter study of the efficacy and safety of prasugrel in pediatric patients with sickle cell anemia utilizing a dose titration strategy. Pediatr Blood Cancer 2016;63 2:299-305. http://www.ncbi.nlm.nih.gov/pubmed/26402148.
  • Kato GJ, Vichinsky E, Galacteros F, Weatherall D, Costa F, Ohene-Frempong K, Krishnamurti L, Smith W, Panepinto J. Sickle Cell Disease for Basic Scientists. Nature Reviews Disease Primers 2016 (in press).
  • Keller S, Longo F, Engelhardt R, Fung EB, Grosse R, Weyhmiller M, Nielsen P, Schoennagel B, Adam G, Fischer R, Yamamura J. Liver and spleen volumetry by ultrasonography and MRI in iron-loading diseases and controls adjusted for body size. J Hepatology 2016 (submitted).
  • Keller S, Longo F, Engelhardt R, Fung EB, Grosse R, Weyhmiller M, Nielsen P, Schoennagel B, Adam G, Fischer R, Yamamura J. Liver and spleen volumetry by MRI and sonography in hematological diseases and normal volumes adjusted for body size. Radiology 2016 (submitted)
  • Khurana M, Fung EB, Vichinsky E, Theil EC. In thalassemia intermedia, dietary non-heme iron is equally bioavailable from ferritin or ferrous sulfate (FeSO4). J Ped Hem Onc 2016 (submitted).
  • Kutny M, Rajpurkar M, Alonzo T, Feusner J, Gregory J. Identification of risk markers for significant bleeding and thrombosis in pediatric Acute Promyelocytic Leukemia: A report from the Children's Oncology Group Study AAML0631. 2016 (submitted).
  • Kutny M, Gregory J, Feusner J. Outcome for Pediatric APL Patients at Children's Oncology Group Sites on the Leukemia Study CALGB 9710. Blood 2016 (submitted).
  • Lal A. Assessment and treatment of pain in thalassemia. Ann N Y Acad Sci 2016;1368 1:65-72. http://www.ncbi.nlm.nih.gov/pubmed/27124110.
  • Lal A, Gomez E, Calloway C. Increased mitochondrial DNA deletions and copy number in transfusion-dependent thalassemia. JCI Insight 2016 (under revision).
  • Lalefar N, Witkowski A, Simonsen JB, Ryan RO. A "Wnt-erized" morphogen transport vehicle induces hematopoietic stem and progenitor cell expansion. Nanomedicine 2016 (submitted).
  • Lee P, Rademaker A, Laonzo T, Feusner J, Hijiya N. Obesity is an adverse prognostic factor in adults but not in children and adolscents with acute promyelocytic leukemia. Blood 2016 (submitted).
  • Liu L, Pertsemlidis A, Ding LH, Story MD, Steinberg MH, Sebastiani P, Hoppe C, Ballas SK, Pace BS. Original Research: A case-control genome-wide association study identifies genetic modifiers of fetal hemoglobin in sickle cell disease. Exp Biol Med (Maywood) 2016;241 7:706-18. http://www.ncbi.nlm.nih.gov/pubmed/27022141.
  • Martin M, Haines D. Clinical Management of Patients With Thalassemia Syndromes. Clin J Oncol Nurs 2016;20 3:310-7. https://cjon.ons.org/cjon/20/3/clinical-management-patients-thalassemia-syndromes.
  • Mulder N, Nembaware V, Adekile A, Anie K, Inusa B, Brown B, Campbell A, Chinenere F, Chunda-Liyoka C, Derebail VK, Geard A, Ghedira K, Hamilton CD, Hanchard NA, Haendel M, Huggins W, Ibrahim M, Jupp S, Kengne-Kamga K, Knight-Malden J, Lopez-Sall P, Mbiyavanga M, Munube D, Niren D, Nnodu OE, Ofori SF, Ohene-Frempong K, Opap K, Panji S, Park M, Pule G, Royal C, Sangeda R, Tayo B, Treadwell M, Tshilolo L, A W. Proceedings of a Sickle Cell Disease Ontology workshop — Towards the first comprehensive ontology for Sickle Cell Disease. Appl Transl Genomics 2016. http://www.sciencedirect.com/science/article/pii/S2212066116300187.
  • Neumayr L, Vichinsky E. Stroke recurrence in adult sickle cell patients: it is time for action! Transfusion 2016;56 5:1001-4. http://www.ncbi.nlm.nih.gov/pubmed/27167352.
  • Paulukonis ST, Eckman JR, Snyder AB, Hagar W, Feuchtbaum LB, Zhou M, Grant AM, Hulihan MM. Defining Sickle Cell Disease Mortality Using a Population-Based Surveillance System, 2004 through 2008. Public Health Rep 2016;131 2:367-75. http://www.ncbi.nlm.nih.gov/pubmed/26957672.
  • Polgreen LE, Vehe R, Rudser K, Kunin-Batson A, Fung EB, Utz J, Dickson P, Shapiro E, Whitley CB. Elevated TNF-alpha is associated with pain and physical disability in mucopolysaccaridosis types I, II and VI. Genetics 2016 (submitted).
  • Rai P, Kelly S, Agrawal AK. Unique aspects of red blood cell transfusion in pediatric patients. Int J Clinical Transf Med 2016;4:43-54.
  • Rai P, Feusner JH. Cerebral Metastasis of Hepatoblastoma: A Review. J Pediatr Hematol Oncol 2016;38 4:279-82. http://www.ncbi.nlm.nih.gov/pubmed/27111454.
  • Rai P. Superior sagittal sinus thrombus in PMH: Case report and review of literature. 2016 (in process).
  • Rai P. Fanconi anemia presentation post-bone marrow transplant in patient with Beta thalassemia major: a case report. 2016 (in process).
  • Shenoy S, Walters MC, Levine JE, Eapen M, Logan B, Panepinto J, Abraham A, Wiedl C. Unrelated donor bone marrow transplantation for children with severe sickle cell disease: results of a phase II trial from the Blood and Marrow Transplant Clinical Trials Network. 2016 (submitted).
  • Singer AW, Selvin S, Block G, Golden C, Carmich SL, Metayer C. Maternal prenatal intake of one-carbon metabolism nutrients and risk of childhood leukemia. Cancer Causes and Control 2016 (accepted).
  • Slater NR, Harmatz P, Higa A, Ng V, Weyhmiller M, Evans P, Porter JB, Sweeters N, Price J, Manji A, Manucha A, Killilea D, Neumayr L, Lal A, Vichinsky E, Walter PB. Granulocyte LewisX (CD15) presentation associates with cardiac iron burden, left ventricular ejection fraction and body mass-index in patients with Beta-thalassemia. 2016 (in process).
  • Slater NR, Porter JB, Evans P, Higa A, Ng V, Weyhmiller M, Sweeters N, Killilea D, Vichinsky E, Harmatz P, Lal A, Walter PB. Increased TLR4 and reactive oxygen production correlate with morphology of THP-1 monocytic cells and peripheral blood monocytes from iron overloaded beta-thalassemia major patients. 2016 (in process).
  • Soupene E, Borja M, Borda M, Larkin S, Kuypers FA. Alterations of LCAT activity and ApoA-I functionality in human sickle blood. Experimental Biology and Medicine 2016 (in press).
  • Soupene E, Kao J, Cheng DH, Wang D, Greninger AL, Knudsen GM, DeRisi JL, Kuypers FA. Association of NMT2 with the acyl-CoA carrier ACBD6 protects the N-myristoyltransferase reaction from palmitoyl-CoA. J Lipid Res 2016;57 2:288-98. http://www.ncbi.nlm.nih.gov/pubmed/26621918.
  • Suh JH, Eltanawy A, Rangan A, Saba JD. A facile stable-isotope dilution method for determination of sphingosine phosphate lyase activity. Chem Phys Lipids 2016;194:101-9. http://www.ncbi.nlm.nih.gov/pubmed/26408264.
  • Sung J, Feusner J. Invasive Rothia Infections in children with Acute Myeloid Leukemia: A report from the Canadian Infections in AML Research Group. Ped Hematology Oncology 2016 (accepted).
  • Sung L, Dix D, Cellot S, Gillmeister B, Ethier MC, Roslin NM, Johnston DL, Feusner J, Mitchell D, Lewis V, Aplenc R, Yanofsky R, Portwine C, Price V, Zelcer S, Silva M, Bowes L, Michon B, Stobart K, Traubici J, Allen U, Beyene J, den Hollander N, Paterson AD. Single nucleotide polymorphism in IL1B is associated with infection risk in paediatric acute myeloid leukaemia. Clin Microbiol Infect 2016. http://www.ncbi.nlm.nih.gov/pubmed/26932518.
  • Thakar MS, Bonfim C, Walters MC, Storb R, Pasquini R, Burroughs L, Sandmaier BM, Woolfrey AE, Kiem H-P. Dose adapted post-transplant cyclophosphamide for HLA-haploidentical transplantation in Fanconi anaemia. 2016 (submitted).
  • Treadwell M, Johnson S, Sisler I, Bitsko M, Gildengorin G, Medina R, Barreda F, Major K, Telfair J, Smith WR. Development of a sickle cell disease readiness for transition assessment. Int J Adolesc Med Health 2016;28 2:193-201. http://www.ncbi.nlm.nih.gov/pubmed/26226115.
  • Trobaugh-Lotrario AD, Meyers RL, Feusner JH. Outcomes of Patients With Relapsed Hepatoblastoma Enrolled on Children's Oncology Group (COG) Phase I and II Studies. J Pediatr Hematol Oncol 2016;38 3:187-90. http://www.ncbi.nlm.nih.gov/pubmed/26583620.
  • Trobaugh-Lotrario AD, Meyers RL, Tiao GM, Feusner JH. Pediatric liver transplantation for hepatoblastoma. Translational Gastroenterology and Hepatology 2016;1 3. Link.
  • Trobaugh-Lotrario A, Feusner J. Unresectable hepatoblastoma: current perspectives. Hepatic Medicine: Evidence and Research 2016 (submitted).
  • Vichinsky E. Non-transfusion-dependent thalassemia and thalassemia intermedia: epidemiology, complications, and management. Curr Med Res Opin 2016;32 1:191-204. http://www.ncbi.nlm.nih.gov/pubmed/26479125.
  • Walter PB, Tirosh O, Sen CK, Packer L, Ames BN. Thiol regulation of mitochondrial function and permeability transition. Mitochondrial stabilizing properties of an amide analogue of R-lipoic acid. 2016 (in process).
  • Walter PB, Godvadze V, Lee S, Ames BN. The conformation of mitochondrial DNA is altered during mitochondrial membrane permeability transition. 2016 (in process).
  • Walter PB, Richter C. Response of mitochondria to iron overload. Increased replication of mitochondrial DNA. 2016 (in process).
  • Walters MC, De Castro LM, Sullivan KM, Krishnamurti L, Kamani N, Bredeson C, Neuberg D, Hassell KL, Farnia S, Campbell A, Petersdorf E. Indications and Results of HLA-Identical Sibling Hematopoietic Cell Transplantation for Sickle Cell Disease. Biol Blood Marrow Transplant 2016;22 2:207-11. http://www.ncbi.nlm.nih.gov/pubmed/26500093.
  • Winstead M, Sun P, Martin K, Earl J, Neumayr L, Hoppe C, Vichinsky E. Enchephaloduroarteriosynangiosis (EDAS) in young patients with sickle cell disease: single-institution experience. 2016 (submitted).
  • Winstead M, Won J, Szuminski M, Michlitsch J, Agrawal A. Febrile neutropenia in pediatric oncology: timing of infectious complications and association with previous infections. 2016 (submitted).
  • Zhang X, Walter PB, Hall SC, Witkowska HE, Shigenaga M. Characterizing the temporal release of mitochondrial proteins by MALDI-TOF following activation of mitochondrial permeability transition. 2016 (in process).
  • Zweideler-McKay P, Hogan MJ, Jubran RF, Black V, Casillas J, Harper J, Malempati S, Margolin J, Felgenhauer J, Frankllin J, Shah M, Seibel N, Buchanan G, Vaiselbuh S, Hastings C, J. H, Stork L. Navigating your career path in pediatric hematology/oncology (PHO): On and off the beaten path. Pediatr Blood Cancer 2016 (submitted)

2015:

  • Ballas SK, Vichinsky EP. Is the medical home for adult patients with sickle cell disease a reality or an illusion? Hemoglobin 2015;39 2:130-3. http://www.ncbi.nlm.nih.gov/pubmed/25806421.
  • Burton BK, Berger KI, Lewis GD, Tarnopolsky M, Treadwell M, Mitchell JJ, Muschol N, Jones SA, Sutton VR, Pastores GM, Lau H, Sparkes R, Genter F, Shaywitz AJ, Harmatz P. Safety and physiological effects of two different doses of elosulfase alfa in patients with morquio a syndrome: A randomized, double-blind, pilot study. Am J Med Genet A 2015;167A 10:2272-81. http://www.ncbi.nlm.nih.gov/pubmed/26069231.
  • Crosby NM, Ghosh M, Su B, Beckstead JA, Kamei A, Simonsen JB, Luo B, Gordon LI, Forte TM, Ryan RO. Anti-CD20 single chain variable antibody fragment-apolipoprotein A-I chimera containing nanodisks promote targeted bioactive agent delivery to CD20-positive lymphomas. Biochem Cell Biol 2015;93 4:343-50. http://www.ncbi.nlm.nih.gov/pubmed/25994015.
  • Day LL, Murray E, Treadwell MJ, Lubin BH. Teaching About Genetics and Sickle Cell Disease in Fifth Grade. Journal of the National Medical Association 2015;Feb 107 (1):4-10. http://www.chori.org/Education/SEPA/Teaching%20Genetics%20and%20SCD_to%20fith%20graders.pdf.
  • Derderian SC, Jeanty C, Walters MC, Vichinsky E, MacKenzie TC. In utero hematopoietic cell transplantation for hemoglobinopathies. Front Pharmacol 2015;5:278. http://www.ncbi.nlm.nih.gov/pubmed/25628564.
  • Erlich HA. HLA typing using next generation sequencing: An overview. Hum Immunol 2015;76 12:887-90. http://www.ncbi.nlm.nih.gov/pubmed/25777625.
  • Forte TM, Ryan RO. Apolipoprotein A5: Extracellular and Intracellular Roles in Triglyceride Metabolism. Curr Drug Targets 2015;16 12:1274-80. http://www.ncbi.nlm.nih.gov/pubmed/26028042.
  • Forte TM, Sharma V, Ryan RO. Apolipoprotein A-V gene therapy for disease prevention / treatment: a critical analysis. J Biomed Res 2015;30. http://www.ncbi.nlm.nih.gov/pubmed/26679785.
  • Fung EB, Gildengorin G, Talwar S, Hagar L, Lal A. Zinc status affects glucose homeostasis and insulin secretion in patients with thalassemia. Nutrients 2015;7 6:4296-307. http://www.ncbi.nlm.nih.gov/pubmed/26043030.
  • Fung EB, Pinal J, Leason M. Reduced Physical Activity Patterns in Patients with Thalassemia Compared to Healthy Controls. J Hematology Oncology Research 2015;2(1)7-21.
  • Gardner K, Hoppe C, Mijovic A, Thein SL. How we treat delayed haemolytic transfusion reactions in patients with sickle cell disease. Br J Haematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25967919.
  • Hagar RW. Teasing Apart Pain in Sickle Cell Disease. Eur J Haematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25645541.
  • Harmatz P, Treadwell M, Burton BK, Mitchell J, Muschol N, Jones S, Pastores G, Lau H, Sparkes R, Sutton VR, Genter F, Haller C, Shaywitz A. Impact of elosulfase alfa on pain in patients with Morquio syndrome type A. Molecular Genetics and Metabolism 2015;114 2:S51-S2. http://www.sciencedirect.com/science/article/pii/S1096719214004843.
  • Hastings C, Gaynon PS, Nachman JB, Sather HN, Lu X, Devidas M, Seibel NL. Increased post-induction intensification improves outcome in children and adolescents with a markedly elevated white blood cell count (>/=200 x 10 /l) with T cell acute lymphoblastic leukaemia but not B cell disease: a report from the Children's Oncology Group. Br J Haematol 2015;168(4):533-46. doi: 10.1111/bjh.13160. Link.
  • Heeney MM, Hoppe CC, Abboud MR, Inusa B, Kanter J, Ogutu B, Brown PB, Heath LE, Jakubowski JA, Zhou C, Zamoryakhin D, Agbenyega T, Colombatti R, Hassab HM, Nduba VN, Oyieko JN, Robitaille N, Segbefia CI, Rees DC, Investigators D. A Multinational Trial of Prasugrel for Sickle Cell Vaso-Occlusive Events. N Engl J Med 2015. http://www.ncbi.nlm.nih.gov/pubmed/26644172.
  • Hoppe CC, Styles L, Heath LE, Zhou C, Jakubowski JA, Winters KJ, Brown PB, Rees DC, Heeney MM. Design of the DOVE (Determining Effects of Platelet Inhibition on Vaso-Occlusive Events) Trial: A Global Phase 3 Double-Blind, Randomized, Placebo-Controlled, Multicenter Study of the Efficacy and Safety of Prasugrel in Pediatric Patients With Sickle Cell Anemia Utilizing a Dose Titration Strategy. Pediatr Blood Cancer 2015. http://www.ncbi.nlm.nih.gov/pubmed/26402148.
  • Ikon N, Su B, Hsu FF, Forte TM, Ryan RO. Exogenous cardiolipin localizes to mitochondria and prevents TAZ knockdown-induced apoptosis in myeloid progenitor cells. Biochem Biophys Res Commun 2015;464 2:580-5. http://www.ncbi.nlm.nih.gov/pubmed/26164234.
  • Kanter J, Telen MJ, Hoppe C, Roberts CL, Kim JS, Yang X. Validation of a novel point of care testing device for sickle cell disease. BMC Med 2015;13:225. http://www.ncbi.nlm.nih.gov/pubmed/26377572.
  • Kelly S, Deng X, Hoppe C, Styles L. A pilot randomized trial of red blood cell transfusion for acute treatment of vaso-occlusive pain episodes in sickle cell anaemia. Br J Haematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25833727.
  • Khurana M, Lee B, Feusner JH. Fever at Diagnosis of Pediatric Acute Lymphoblastic Leukemia: Are Antibiotics Really Necessary? J Pediatr Hematol Oncol 2015;37 7:498 -501. http://www.ncbi.nlm.nih.gov/pubmed/26376233.
  • Kim H, Erlich HA, Calloway CD. Analysis of mixtures using next generation sequencing of mitochondrial DNA hypervariable regions. Croat Med J 2015;56 3:208-17. http://www.ncbi.nlm.nih.gov/pubmed/26088845.
  • Kumar A, Saba JD. Regulation of immune cell trafficking by sphingosine-1-phosphate. Cell Mol Biol 2015;61 2. Link.
  • Lal A, Patterson L, Goldrich A, Marsh A. Point-of-care end-tidal carbon monoxide reflects severity of hemolysis in sickle cell anemia. Pediatr Blood Cancer 2015;62 5:912-4. http://www.ncbi.nlm.nih.gov/pubmed/25683629.
  • Lee DW, Doh I, Kuypers FA, Cho YH. Sub-population analysis of deformability distribution in heterogeneous red blood cell population. Biomed Microdevices 2015;17 6:102. http://www.ncbi.nlm.nih.gov/pubmed/26383009.
  • Marsh A, Schiffelers R, Kuypers F, Larkin S, Gildengorin G, van Solinge W, Hoppe C. Microparticles as biomarkers of osteonecrosis of the hip in sickle cell disease. Br J Haematol 2015;168 1:135-8. http://www.ncbi.nlm.nih.gov/pubmed/25196812.
  • McCann JC, Shigenaga MK, Mietus-Snyder ML, Lal A, Suh JH, Krauss RM, Gildengorin GL, Goldrich AM, Block DS, Shenvi SV, McHugh TH, Olson DA, Ames BN. A multicomponent nutrient bar promotes weight loss and improves dyslipidemia and insulin resistance in the overweight/obese: chronic inflammation blunts these improvements. FASEB J 2015;29 8:3287-301. http://www.ncbi.nlm.nih.gov/pubmed/25900806.
  • Meloni A, Detterich J, Pepe A, Harmatz P, Coates TD, Wood JC. Pulmonary hypertension in well-transfused thalassemia major patients. Blood Cells Mol Dis 2015;54 2:189-94. http://www.ncbi.nlm.nih.gov/pubmed/25488617.
  • Morris CR, Kim HY, Klings ES, Wood J, Porter JB, Trachtenberg F, Sweeters N, Olivieri NF, Kwiatkowski JL, Virzi L, Hassell K, Taher A, Neufeld EJ, Thompson AA, Larkin S, Suh JH, Vichinsky EP, Kuypers FA, Thalassemia Clinical Research N. Dysregulated arginine metabolism and cardiopulmonary dysfunction in patients with thalassaemia. Br J Haematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25907665.
  • Qayed M, Khurana M, Hilinski J, Gillespie S, McCracken C, Applegate K, Chiang K-Y, Horan J. Risk for CMV reactivation in children undergoing allogeneic hematopoietic stem cell transplantation. Pediatric Blood & Cancer 2015;62 2:364-6. http://onlinelibrary.wiley.com/doi/10.1002/pbc.25237/abstract.
  • Ryan RO. Metabolic annotation of 2-ethylhydracrylic acid. Clin Chim Acta 2015;448:91-7. http://www.ncbi.nlm.nih.gov/pubmed/26115894.
  • Saba JD. A B cell-dependent mechanism restrains T cell transendothelial migration. Nat Med 2015;21 5:424-6. http://www.ncbi.nlm.nih.gov/pubmed/25951526.
  • Schiffman M, Burk RD, Boyle S, Raine-Bennett T, Katki HA, Gage JC, Wentzensen N, Kornegay JR, Aldrich C, Tam T, Erlich H, Apple R, Befano B, Castle PE. A study of genotyping for management of human papillomavirus-positive, cytology-negative cervical screening results. J Clin Microbiol 2015;53 1:52-9. Link.
  • Singer ST, Killilea D, Suh JH, Wang ZJ, Yuan Q, Ivani K, Evans P, Vichinsky E, Fischer R, Smith JF. Fertility in transfusion-dependent thalassemia men: effects of iron burden on the reproductive axis. Am J Hematol 2015;90 9:E190-2. http://www.ncbi.nlm.nih.gov/pubmed/26044409.
  • Soupene E, Kuypers FA. Ligand binding to the ACBD6 protein regulates the acyl-CoA transferase reactions in membranes. J Lipid Res 2015;56 10:1961-71. http://www.ncbi.nlm.nih.gov/pubmed/26290611.
  • Soupene E, Wang D, Kuypers FA. Remodeling of host phosphatidylcholine by Chlamydia acyltransferase is regulated by acyl-CoA binding protein ACBD6 associated with lipid droplets. Microbiologyopen 2015. http://www.ncbi.nlm.nih.gov/pubmed/25604091.
  • Suh JH, Saba JD. Sphingosine-1-phosphate in inflammatory bowel disease and colitis-associated colon cancer: the fat's in the fire. Transl Cancer Res 2015;4 5:469-83. http://www.ncbi.nlm.nih.gov/pubmed/27011900.
  • Tang H, Ho H, Wu P, Chen S, Kuypers FA, Cheng M, Chiu DT. Inability to Maintain GSH Pool in G6PD-Deficient Red Cells Causes Futile AMPK Activation and Irreversible Metabolic Disturbance. Antioxid Redox Signal 2015. http://www.ncbi.nlm.nih.gov/pubmed/25556665.
  • Treadwell M, Johnson S, Sisler I, Bitsko M, Gildengorin G, Medina R, Barreda F, Major K, Telfair J, Smith WR. Development of a sickle cell disease readiness for transition assessment. Int J Adolesc Med Health 2015. http://www.ncbi.nlm.nih.gov/pubmed/26226115.
  • Treadwell M, Johnson S, Sisler I, Bitsko M, Gildengorin G, Medina R, Barreda F, Major K, Telfair J, Smith WR. Self-efficacy and readiness for transition from pediatric to adult care in sickle cell disease. Int J Adolesc Med Health 2015. http://www.ncbi.nlm.nih.gov/pubmed/26226116.
  • Treadwell MJ, Anie KA, Grant AM, Ofori-Acquah SF, Ohene-Frempong K. Using Formative Research to Develop a Counselor Training Program for Newborn Screening in Ghana. J Genet Couns 2015;24 2:267-77. http://www.ncbi.nlm.nih.gov/pubmed/25193810.
  • Treadwell MJ, Barreda F, Kaur K, Gildengorin G. Emotional distress, barriers to care and health-related quality of life in sickle cell disease. J Clin Outcomes Manage 2015;22 1:10-20. http://www.turner-white.com/pdf/jcom_jan15_sickle.pdf.
  • Trobaugh-Lotrario AD, Meyers RL, Feusner JH. Outcomes of Patients With Relapsed Hepatoblastoma Enrolled on Children's Oncology Group (COG) Phase I and II Studies. J Pediatr Hematol Oncol 2015. http://www.ncbi.nlm.nih.gov/pubmed/26583620.
  • Tubman VN, Fung EB, Vogiatzi M, Thompson AA, Rogers ZR, Neufeld EJ, Kwiatkowski JL, Thalassemia Clinical Research N. Guidelines for the Standard Monitoring of Patients With Thalassemia: Report of the Thalassemia Longitudinal Cohort. J Pediatr Hematol Oncol 2015;37 3:e162-9. http://www.ncbi.nlm.nih.gov/pubmed/26201037.
  • Walters MC. Update of hematopoietic cell transplantation for sickle cell disease. Curr Opin Hematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25767957.
  • Walters MC, De Castro LM, Sullivan KM, Krishnamurti L, Kamani N, Bredeson C, Neuberg D, Hassell KL, Farnia S, Campbell A, Petersdorf E. Indications and Results of HLA-Identical Sibling Hematopoietic Cell Transplantation for Sickle Cell Disease. Biol Blood Marrow Transplant 2015. http://www.ncbi.nlm.nih.gov/pubmed/26500093.
  • Walters MC, MacKenzie TC. A booster shot to cure hemoglobinopathies. Blood 2015;126 10:1159-61. http://www.ncbi.nlm.nih.gov/pubmed/26337353.
  • Witkowski A, Krishnamoorthy A, Su B, Beckstead JA, Ryan RO. Isolation and characterization of recombinant murine Wnt3a. Protein Expr Purif 2015;106:41-8. http://www.ncbi.nlm.nih.gov/pubmed/25448592.
  • Wonkam A, Makani J, Ofori-Aquah S, Nnodu OE, Treadwell M, Royal C, Ohene-Frempong K, as members of the HAC. Sickle cell disease and H3Africa: enhancing genomic research on cardiovascular diseases in African patients. Cardiovasc J Afr 2015;26 2 Suppl 1:S50-5. http://www.ncbi.nlm.nih.gov/pubmed/25962948.
  • Yalcin O, Oronsky B, Carvalho LJ, Kuypers FA, Scicinski J, Cabrales P. From METS to malaria: RRx-001, a multi-faceted anticancer agent with activity in cerebral malaria. Malar J 2015;14:218. http://www.ncbi.nlm.nih.gov/pubmed/26017006.
  • Yamamoto F, Hoglund B, Fernandez-Vina M, Tyan D, Rastrou M, Williams T, Moonsamy P, Goodridge D, Anderson M, Erlich HA, Holcomb CL. Very high resolution single pass HLA genotyping using amplicon sequencing on the 454 next generation DNA sequencers: Comparison with Sanger sequencing. Hum Immunol 2015;76 12:910-6. http://www.ncbi.nlm.nih.gov/pubmed/26037172.
  • Zhang L, Samad A, Pombo-de-Oliveria MS, Scelo G, Smith MT, Feusner J, Wiemels JL, Metayer C. Global characteristics of childhood acute promyelocytic leukemia. Blood Reviews 2015;29(2) March 2015:101-25. Link.
  • Zerofsky M, Ryder M, Bhatia S, Stephensen CB, King J, Fung EB. Effects of early vitamin D deficiency rickets on bone and dental health, growth and immunity. Matern Child Nutr 2015. http://www.ncbi.nlm.nih.gov/pubmed/25850574.

2014:

  • Afshar M, Birnbaum D, Golden C. Review of dextromethorphan administration in 18 patients with subacute methotrexate central nervous system toxicity. Pediatr Neurol 2014;50 6:625-9. http://www.ncbi.nlm.nih.gov/pubmed/24742799.
  • Afzal SY, Wender AR, Jones MD, Fung EB, Pico EL. The effect of low magnitude mechanical stimulation (LMMS) on bone density in patients with Rett syndrome: a pilot and feasibility study. J Pediatr Rehabil Med 2014;7 2:167-78. http://www.ncbi.nlm.nih.gov/pubmed/25096869.
  • Calloway CD. Resolution of DNA mixtures and analysis of degraded DNA using the 454 DNA sequencing technology. National Criminal Justice Reference Service, technical report, NIJ #2010-DN-BX-K141 2014:141. Link.
  • Cui J, Azimi M, Hoppe CC. Detection of a novel betadelta-globin fusion gene, anti-lepore Hb CHORI (beta(through IVS-I-57)/delta(from IVS-I-101)), by multiplex ligation-dependent probe amplification. Hemoglobin 2014;38 1:60-3. http://www.ncbi.nlm.nih.gov/pubmed/24102354.
  • Dagri JN, Evans A, Torkildson JC, Portnow J, Ashby LS, Zakotnik B, Brown RJ, Dhall G, Finlay JL. Feasibility of an Attenuated Maintenance chemotherapy Regimen Directed at Adolescents and Young Adults with Newly Diagnosed Localized Medulloblastoma and Other Central Nervous System Embryonal Tumors. J Adolescent and Young Adult Oncology 2014;3 3:106-11.
  • Dang DN, Morris HD, Feusner JH, Koduru P, Wilson K, Timmons CF, Cavalier M, Luu HS. Therapy-induced Secondary Acute Myeloid Leukemia With t(11;19)(q23;p13.1) in a Pediatric Patient With Relapsed Acute Promyelocytic Leukemia. J Pediatr Hematol Oncol 2014;36 8:e546-8. http://www.ncbi.nlm.nih.gov/pubmed/24942021.
  • Ghosh M, Ren G, Simonsen JB, Ryan RO. Cationic lipid nanodisks as an siRNA delivery vehicle. Biochem Cell Biol 2014;92 3:200-5. http://www.ncbi.nlm.nih.gov/pubmed/24840721.
  • Ghosh M, Ryan RO. Curcumin homing to the nucleolus: mechanism for initiation of an apoptotic program. J Nutr Biochem 2014;25 11:1117-23. http://www.ncbi.nlm.nih.gov/pubmed/25172633.
  • Ghosh M, Ryan RO. ApoE enhances nanodisk-mediated curcumin delivery to glioblastoma multiforme cells. Nanomedicine (Lond) 2014;9 6:763-71. http://www.ncbi.nlm.nih.gov/pubmed/23879635.
  • Gladwin MT, Barst RJ, Gibbs JS, Hildesheim M, Sachdev V, Nouraie M, Hassell KL, Little JA, Schraufnagel DE, Krishnamurti L, Novelli E, Girgis RE, Morris CR, Berman Rosenzweig E, Badesch DB, Lanzkron S, Castro OL, Taylor JGt, Goldsmith JC, Kato GJ, Gordeuk VR, Machado RF, Walk Phaast investigators. Risk factors for death in 632 patients with sickle cell disease in the United States and United Kingdom. PloS one. 2014;9(7):e99489. Epub 2014/07/06. doi: 10.1371/journal.pone.0099489. PubMed PMID: 24988120; PubMed Central PMCID: PMC4079316. http://journals.plos.org/plosone/article?id=10.1371/journal.pone.0099489.
  • Green ST, Martin MB, Haines D, Carson S, Coates T, Oliveros O, Gerstenberger E, Trachtenberg F, Kwiatkowski JL, Thalassaemia Clinical Research N. Variance of pain prevalence and associated severity during the transfusion cycle of adult thalassaemia patients. Br J Haematol 2014;166 5:797-800. http://www.ncbi.nlm.nih.gov/pubmed/24805301.
  • Holcomb CL, Rastrou M, Williams TC, Goodridge D, Lazaro AM, Tilanus M, Erlich HA. Next-generation sequencing can reveal in vitro-generated PCR crossover products: some artifactual sequences correspond to HLA alleles in the IMGT/HLA database. Tissue Antigens 2014;83 1:32-40. http://www.ncbi.nlm.nih.gov/pubmed/24355006.
  • Hoppe CC. Inflammatory mediators of endothelial injury in sickle cell disease. Hematol Oncol Clin North Am 2014;28 2:265-86. http://www.ncbi.nlm.nih.gov/pubmed/24589266.
  • Karafin MS, Graminske S, Erickson P, Walters MC, Scott EP, Carter S, Padmanabhan A. Evaluation of the Spectra Optia apheresis system for mononuclear cell (MNC) collection in G-CSF mobilized and nonmobilized healthy donors: results of a multicenter study. J Clin Apher 2014;29 5:273-80. http://www.ncbi.nlm.nih.gov/pubmed/24677347.
  • Karski EE, Dvorak CC, Leung W, Miller W, Shaw PJ, Qayed M, Katsanis E, Feusner JH. Treatment of Hepatoblastoma With High-dose Chemotherapy and Stem Cell Rescue: The Pediatric Blood and Marrow Transplant Consortium Experience and Review of the Literature. J Pediatr Hematol Oncol 2014. http://www.ncbi.nlm.nih.gov/pubmed/24577552.
  • Keller SD, Yang M, Treadwell MJ, Werner EM, Hassell KL. Patient reports of health outcome for adults living with sickle cell disease: development and testing of the ASCQ-Me item banks. Health Qual Life Outcomes 2014;12:125. http://www.ncbi.nlm.nih.gov/pubmed/25146160.
  • Klaassen RJ, Barrowman N, Merelles-Pulcini M, Vichinsky E, Sweeters N, Kirby-Allen M, Neufeld EJ, Kwiatkowski JL, Wu J, Vickars L, Blanchette VS, Forgie M, Yamashita R, Wong-Rieger D, Young NL. Validation and reliability of a disease-specific quality of life measure (the TranQol) in adults and children with thalassaemia major. Br J Haematol 2014;164 3:431-7. http://www.ncbi.nlm.nih.gov/pubmed/24180641.
  • Kutny MA, Gregory J, Jr., Feusner JH. Treatment of paediatric APL: how does the therapeutic approach differ from adults? Best Pract Res Clin Haematol 2014;27 1:69-78. http://www.ncbi.nlm.nih.gov/pubmed/24907019.
  • Kuypers FA. Hemoglobin S Polymerization and Red Cell Membrane Changes. Hematol Oncol Clin North Am 2014;28 2:155-79. http://www.ncbi.nlm.nih.gov/pubmed/24589260.
  • Lin L, Ma C, Wei B, Aziz N, Rajalingam R, Yusung S, Erlich HA, Trachtenberg EA, Targan SR, McGovern DP, Heath JR, Braun J. Human NK cells licensed by killer Ig receptor genes have an altered cytokine program that modifies CD4+ T cell function. J Immunol 2014;193 2:940-9. http://www.ncbi.nlm.nih.gov/pubmed/24935928.
  • Mackin RS, Insel P, Truran D, Vichinsky E, Neumayr LD, Armstrong FD, Gold JI, Kesler K, Brewer J, Weiner MW, Neuropsychological D, Neuroimaging Adult Sickle Cell Anemia Study G. Neuroimaging abnormalities in adults with sickle cell anemia: associations with cognition. Neurology 2014;82 10:835-41. http://www.ncbi.nlm.nih.gov/pubmed/24523480.
  • Marsh A, Golden C, Hoppe C, Quirolo K, Vichinsky E. Renal medullary carcinoma in an adolescent with sickle cell anemia. Pediatr Blood Cancer 2014;61 3:567. http://www.ncbi.nlm.nih.gov/pubmed/24108577.
  • Paulukonis ST, Harris WT, Coates TD, Neumayr L, Treadwell M, Vichinsky E, Feuchtbaum LB. Population based surveillance in sickle cell disease: Methods, findings and implications from the California registry and surveillance system in hemoglobinopathies project (RuSH). Pediatr Blood Cancer 2014;61 12:2271-6. http://www.ncbi.nlm.nih.gov/pubmed/25176145.
  • Polgreen LE, Thomas W, Fung E, Viskochil D, Stevenson DA, Steinberger J, Orchard P, Whitley CB, Ensrud KE. Low Bone Mineral Content and Challenges in Interpretation of Dual-Energy X-Ray Absorptiometry in Children With Mucopolysaccharidosis Types I, II, and VI. J Clin Densitom 2014;17 1:200-6. http://www.ncbi.nlm.nih.gov/pubmed/23562131.
  • Porter JB, Walter PB, Neumayr LD, Evans P, Bansal S, Garbowski M, Weyhmiller MG, Harmatz PR, Wood JC, Miller JL, Byrnes C, Weiss G, Seifert M, Grosse R, Grabowski D, Schmidt A, Fischer R, Nielsen P, Niemeyer C, Vichinsky E. Mechanisms of plasma non-transferrin bound iron generation: insights from comparing transfused diamond blackfan anaemia with sickle cell and thalassaemia patients. Br J Haematol 2014;167 5:692-6. http://www.ncbi.nlm.nih.gov/pubmed/25209728.
  • Puri L, Saba J. Getting a Clue from 1q: Gain of Chromosome 1q in Cancer. J Cancer Biol Res 2014; 2(3): 1053. Link.
  • Quirolo K, Bertolone S, Hassell K, Howard T, King KE, Rhodes DK, Bill J. The evaluation of a new apheresis device for automated red blood cell exchange procedures in patients with sickle cell disease. Transfusion 2014. http://www.ncbi.nlm.nih.gov/pubmed/25330984.
  • Reid ME, Halter Hipsky C, Hue-Roye K, Hoppe C. Genomic analyses of RH alleles to improve transfusion therapy in patients with sickle cell disease. Blood Cells Mol Dis 2014;52 4:195-202. http://www.ncbi.nlm.nih.gov/pubmed/24309423.
  • Singer ST, Kuypers F, Fineman J, Gildengorin G, Larkin S, Sweeters N, Rosenfeld H, Kurio G, Higa A, Jeng M, Huang J, Vichinsky E. Elevated tricuspid regurgitant jet velocity in subgroups of thalassemia patients: insight into pathophysiology and the effect of splenectomy. Ann Hematol 2014;93 7:1139-48. http://www.ncbi.nlm.nih.gov/pubmed/24577514.
  • Soni S, Boulad F, Cowan MJ, Scaradavou A, Dahake J, Edwards S, Walters MC. Combined umbilical cord blood and bone marrow from HLA-identical sibling donors for hematopoietic stem cell transplantation in children with hemoglobinopathies. Pediatr Blood Cancer 2014;61 9:1690-4. http://www.ncbi.nlm.nih.gov/pubmed/24803091.
  • Stevenson DA, Rudser K, Kunin-Batson A, Fung EB, Viskochil D, Shapiro E, Orchard PJ, Whitley CB, Polgreen LE. Biomarkers of bone remodeling in children with mucopolysaccharidosis types I, II, and VI. J Pediatr Rehabil Med 2014;7 2:159-65. http://www.ncbi.nlm.nih.gov/pubmed/25096868.
  • Suh JH, Saba JD. Tracking hippo in the cancer jungle. Chem Biol 2014;21 7:803-4. http://www.ncbi.nlm.nih.gov/pubmed/25036773.
  • Suh J, Kanathezhath B, Shenvi S, Guo H, Zhou A, Tiwana A, Kuypers F, Ames B, Walters M. Thiol/Redox Metabolomic Profiling Implicates GSH Dysregulation in Early Experimental Graft versus Host Disease (GVHD). PLoS ONE 2014;9 (2):e88868. http://www.plosone.org/article/info%3Adoi%2F10.1371%2Fjournal.pone.0088868.
  • Te Vruchte D, Speak AO, Wallom KL, Al Eisa N, Smith DA, Hendriksz CJ, Simmons L, Lachmann RH, Cousins A, Hartung R, Mengel E, Runz H, Beck M, Amraoui Y, Imrie J, Jacklin E, Riddick K, Yanjanin NM, Wassif CA, Rolfs A, Rimmele F, Wright N, Taylor C, Ramaswami U, Cox TM, Hastings C, Jiang X, Sidhu R, Ory DS, Arias B, Jeyakumar M, Sillence DJ, Wraith JE, Porter FD, Cortina-Borja M, Platt FM. Relative acidic compartment volume as a lysosomal storage disorder-associated biomarker. J Clin Invest 2014. http://www.ncbi.nlm.nih.gov/pubmed/24487591.
  • Theil EC. IRE mRNA riboregulators use metabolic iron (Fe) to control mRNA activity and iron chemistry in animals. Metallomics 2014. http://www.ncbi.nlm.nih.gov/pubmed/25209685.
  • Trachtenberg FL, Gerstenberger E, Xu Y, Mednick L, Sobota A, Ware H, Thompson AA, Neufeld EJ, Yamashita R, Thalassemia Clinical Research N. Relationship among chelator adherence, change in chelators, and quality of life in thalassemia. Qual Life Res 2014;23 8:2277-88. http://www.ncbi.nlm.nih.gov/pubmed/24682717.
  • Treadwell MJ, Anie KA, Grant AM, Ofori-Acquah SF, Ohene-Frempong K. Using Formative Research to Develop a Counselor Training Program for Newborn Screening in Ghana. J Genet Couns 2014. http://www.ncbi.nlm.nih.gov/pubmed/25193810.
  • Treadwell MJ, Bell M, Leibovich SA, Barreda F, Marsh A, Gildengorin G, Morris CR. A Quality Improvement Initiative to Improve Emergency Department Care for Pediatric Patients with Sickle Cell Disease. J Clin Outcomes Manage 2014;21 2:62-70. http://www.hospitalphysician.com/pdf/jcom_feb14_pediatric.pdf.
  • Treadwell MJ, Hassell K, Levine R, Keller S. Adult Sickle Cell Quality of Life Measurement Information System (ASCQ-Me): Conceptual Model Based on Review of the Literature and Formative Research. Clin J Pain 2014. http://www.ncbi.nlm.nih.gov/pubmed/24300219.
  • Trobaugh-Lotrario AD, Venkatramani R, Feusner JH. Hepatoblastoma in Children With Beckwith-Wiedemann Syndrome: Does it Warrant Different Treatment? J Pediatr Hematol Oncol 2014. http://www.ncbi.nlm.nih.gov/pubmed/24608075.
  • Ubogy S, Olson K. The Trauma Symptom Checklist for Children and Misdiagnosis of PTSD in A Youth with Acute Lymphocytic Leukemia: A Brief Report. Journal of Child & Adolescent Trauma 2014:1-3. http://rd.springer.com/article/10.1007/s40653-014-0004-1
  • Vichinsky E, Neumayr L, Trimble S, Giardina PJ, Cohen AR, Coates T, Boudreaux J, Neufeld EJ, Kenney K, Grant A, Thompson AA, Investigators CDCT. Transfusion complications in thalassemia patients: a report from the Centers for Disease Control and Prevention (CME). Transfusion 2014;54 4:972-81; quiz 1. http://www.ncbi.nlm.nih.gov/pubmed/23889533.
  • Wagner JE, Jr., Eapen M, Carter S, Wang Y, Schultz KR, Wall DA, Bunin N, Delaney C, Haut P, Margolis D, Peres E, Verneris MR, Walters M, Horowitz MM, Kurtzberg J, Blood, Marrow Transplant Clinical Trials N. One-unit versus two-unit cord-blood transplantation for hematologic cancers. N Engl J Med 2014;371 18:1685-94. http://www.ncbi.nlm.nih.gov/pubmed/25354103.
  • Walters MC. Update of hematopoietic cell transplantation for sickle cell disease. Curr Opin Hematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25767957.
  • Wun T, Styles L, DeCastro L, Telen MJ, Kuypers F, Cheung A, Kramer W, Flanner H, Rhee S, Magnani JL, Thackray H. Phase 1 study of the E-selectin inhibitor GMI 1070 in patients with sickle cell anemia. PLoS One 2014;9 7:e101301. http://www.ncbi.nlm.nih.gov/pubmed/24988449.
  • Zaky W, Dhall G, Ji L, Haley K, Allen J, Atlas M, Bertolone S, Cornelius A, Gardner S, Patel R, Pradhan K, Shen V, Thompson S, Torkildson J, Sposto R, Finlay JL. Intensive induction chemotherapy followed by myeloablative chemotherapy with autologous hematopoietic progenitor cell rescue for young children newly-diagnosed with central nervous system atypical teratoid/rhabdoid tumors: the Head Start III experience. Pediatr Blood Cancer 2014;61 1:95-101. http://www.ncbi.nlm.nih.gov/pubmed/23934933.

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Editorials:

2015:

2014:


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Letters/Commentary:

2016:

  • Rai P, Vichinsky E. Commentary: Debaun M, et al. Controlled Trial of Transfusions for Silent Cerebral Infarcts in Sickle Cell Anemia. In: Yearbook of Pediatrics; Cabana MD, ed; Elsevier 2016.

2014:

  • Klings ES, Machado RF, Morris CR, Gordeuk VR, Kato GJ, Ataga KI, Castro O, Hsu L, Telen MJ, Krishnamurti L, Steinberg MH, Gladwin MT, Diagnosis ATSCGft, Treatment of Pulmonary Hypertension in Sickle Cell Disease C. Reply: Practice guideline for pulmonary hypertension in sickle cell: direct evidence needed before universal adoption. Am J Respir Crit Care Med. 2014;190(2):238-40. Epub 2014/07/16. doi: 10.1164/rccm.201404-0733LE. PubMed PMID: 25025360; PubMed Central PMCID: PMC4226058. a href="http://www.atsjournals.org/doi/abs/10.1164/rccm.201404-0733LE#.VLXc-yvF_Tc.
  • Klings ES, Vichinsky E, Morris CR. Response to "Efficacy and safety of sildenafil for the treatment of severe pulmonary hypertension in patients with hemoglobinopathies: results from a long-term follow up " Haematologica 2014;99(2):e17-18. Haematologica 2014;99 2:e19. http://www.ncbi.nlm.nih.gov/pubmed/24497564.
  • Klings ES, Morris CR, Hsu LL, Castro O, Gladwin MT, Mubarak KK. Pulmonary hypertension of sickle cell disease beyond classification constraints. J Am Coll Cardiol 2014;63 25 Pt A:2881-2. http://www.ncbi.nlm.nih.gov/pubmed/24794120.
  • Puri L, Hastings C. Eosinophilia, Thrombosis, and Arthralgia in a 4-Year-Old Girl. ASPHO e-newsletter, July 2014.
  • Reddy-Holdcraft S, Mehta PS, Agrawal AK. Paclitaxel for relapsed or recurrent HIV-associated pediatric Kaposi's sarcoma. AIDS 2014;28 5:800-2. http://www.ncbi.nlm.nih.gov/pubmed/24983546.
  • Slone JS, Agrawal AK, Mehta PS, Mazhani L, Motumise K, Anabwani G, Poplack DG. Reply to "Childhood Cancer in Africa". Pediatr Blood Cancer 2014;61 8:1524. http://www.ncbi.nlm.nih.gov/pubmed/24519963.

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Abstracts:

2016:

  • Hankin D, Raphael R, Feusner JH. Long-term Follow-up for Young Adult Survivors of Pediatric Cancer: Successful Transition of Care. American Psychological Oncology Society 13th Annual Conference. San Diego, CA; March 2016. Psycho-Oncology 25(S2): 148.
  • Hastings C, Liu B, Vieira C, Lourenco C, Almeida ML, Williams DC, Plummer E, Wang RY, Casey A, Bodamer O, Bascon C, Hrynkow S. Management of Niemann-Pick Disease Type C with intravenous hydroxypropyl-beta-cyclodextrin: Clinical experience in 11 patients. Ara Parseghian Medical Research Foundation Annual Conference. Tucson, Arizona, June 4-7, 2016. Link.
  • Heeney M, Hoppe C, Abboud M, Inusa B, Kanter J, Ogutu B, Brown P, Heath L, Jakubowski J, Zhou C, Zamoryakhin D, Agbenyega T, Columbatti R, Hassab H, Nduba V, Oyieko J, Robitaille N, Segbefia C, Rees D. Determining Effects of Platelet Inhibition on Vaso-occlusive Events (DOVE) Trial: A Double-Blind, Placebo-Controlled Study of Prasugrel in Paediatric Patients with Sickle Cell Anaemia. European Hematology Association, 21st Congress. Copenhagen, Denmark June 9-12, 2016.
  • Lal A, Smith K, Marsh A, Neumayr L. Point-of-Care Screening for Sickle Cell Anemia with an End-Tital Carbon Monoxide Monitor. PAS Annual Meeting. Baltimore, MD; Apr 30-May 3, 2016.
  • Lew G, Lu X, Yanofsky R, Rheingold SR, Whitlock JA, Wang C, Devidas M, Hastings CA, Winick NJ, Carroll WL, Borowitz MA, Pulsipher M, Hunger SP. Race and ethnicity do not impact outcomes after relapse of childhood B-lymphoblastic leukemia: a report from Children's Oncology Group (COG) study AALL0433. ASPHO 29th Annual Meeting. Minneapolis, MN; May 11-14, 2016. Pediatric Blood & Cancer Poster #512. Link.
  • Michlitsch J, Braga L, Rodrigo R, Gupta A, Lorenzo A. Minimally invasive surgical resection and buccal graft vaginoplasty without radiotherapy (rt) for definitive local control in girls with vaginal botryoid rhabdomyosarcoma (RMS). ASPHO 29th Annual Meeting. Minneapolis, MN; May 11-14, 2016. Pediatric Blood & Cancer Poster #784. Link.
  • Nichols T, Lanning M, Sinclair-Hart L, Dessie A, Chaconas E, Agrawal A. Clinical outcomes of pediatric patients with fever and suspected neutropenia in the emergency department--does time to antibiotic administration matter? ASPHO 29th Annual Meeting. Minneapolis, MN; May 11-14, 2016. Pediatric Blood & Cancer Poster #661. Link.
  • Rai P, Feusner J, Agrawal AK. Risk of intrathecal methotrexate neurotoxicity and subsequent isolated central nervous system relapse in pediatric pre-B acute lymphoblastic leukemia. ASPHO 29th Annual Meeting. Minneapolis, MN; May 11-14, 2016. Pediatric Blood & Cancer,Poster #587. Link.
  • Rai P. Exploratory study investigating the role of Sirtuin-3 in ameliorating radiation induced late bone marrow injury. Poster, Pediatric Blood and Marrow Transplant Consortium (PBMTC), ASPHO 29th Annual Meeting. Minneapolis, MN; May 11-14, 2016.
  • Treadwell M, Anie K, Lamptey M, Dennis-Antwi JA, Kissiwah M, Ofori-Acquah A, Ampomah M, Ojodu J, Yusuf C, Grant A, OheneFrempong K. Development of a course to train health care providers in the delivery of genetic education and counseling for sickle cell conditions in Ghana (GENECIS-GHANA). 10th Annual Sickle Cell Disease Research and Educational Symposium and 39th National Sickle Cell Disease Scientific Meeting. Fort Lauderdale, FL; April 15-18, 2016. Foundation for Sickle Cell Disease Research, #JSCDH-D-16-00066. Link.
  • Trobaugh-Lotrario AD, Feusner J. Clinical Characteristics of Patients with Familial Adenomatous Polyposis (FAP) and Hepatoblastoma (HB) International Pediatric Liver Tumor Symposium. Houston, Texas; Feb 25-26, 2016. Texas Children's Hospital.
  • Vichinsky E, El Beshlawy A, Alzoebia A, Kamdem A, Koussa S, Chotsampancharoen T, Bruederle A, Gilotti G, Han JM, Elalfy M. Long-Term Safety and Efficacy of Deferasirox in Pediatric Patients with Transfusional Hemosiderosis: Results From a 5-Year Observational Study (ENTRUST). 21st Congress of the European Hematology Association; Copenhagen, Denmark; June 9-12, 2016; E-poster presentation #E1480. Link.
  • Walter PB, Curtis C, Hodge M, Razavi M, Minkley M, Lal A, Higa A, Killilea D, Pearson T, Fung E. Effect of zinc supplementation on glucose metabolism, oxidative stress and iron trafficking proteins in transfusion dependent patients with thalassemia. 21st Congress of the European Hematology Association. EHA Learning Center #E1490, Copenhagen, Denmark; June 9-12, 2016. Link.
  • Walton A, Brinkman W, Shook L, Treadwell M, Mosley C, Peugh J, Kallinyak K, Saving K, Whitten-Shurney W, Ware R, Crosby L. Shared decision making for hydroxyurea with families of patients with sickle cell anemia. 10th Annual Sickle Cell Disease Research and Educational Symposium and 39th National Sickle Cell Disease Scientific Meeting. Fort Lauderdale, FL; April 15-18, 2016. Foundation for Sickle Cell Disease Research, #JSCDH-D-16-00086. Link.
  • Weyhmiller M, Vega B, Padua E, Hitt D, Harmatz P, Fischer R. Iron and Fat Quantification by MRI R2*: a Phantom Study. European Iron Club Meeting. April 7-10, 2016.
  • Winstead M, Won J, Szuminski M, Pariury H, Michlitsch J, Agrawal AK. Febrile neutropenia in children with cancer: the role of hospitalization until fever resolution. ASPHO 29th Annual Meeting. Minneapolis, MN; May 11-14, 2016. Pediatric Blood & Cancer, Poster #655. Link.
  • Winstead M, Sun P, Martin K, Earl J, Neumayr L, Hoppe C, Vichinsky E. Encephaloduroarteriosynangiosis (EDAS) in young patients with sickle cell disease: single-institution experience. 10th Annual Sickle Cell Disease Research and Educational Symposium and 39th National Sickle Cell Disease Scientific Meeting. Fort Lauderdale, FL; April 15-18, 2016. Foundation for Sickle Cell Disease Research, #JSCDH-D-16-00005. Link.

2015:

  • Badaway S, Vaiselbuh S, Meier ER, Pinkney K, Myers K, Black V, Hastings C, Hilden J, Zweidler-McKay PA, Stork L, Johnson TS. The interim analysis of the ASPHO mentoring program: Two-year outcomes. ASPHO 28th Annual Meeting. Phoenix, AZ; May 6-9, 2015. Pediatric Blood & Cancer 62(S2); Oral presentation. Link.
  • Cappelli B, Bernaudin F, Ruggeri A, Labopin M, Volt F, Simoes BP, Ferster A, Dupont S, de la Fuente J, Dalle J-H, Zecca M, Robin M, Walters MC, Dhedin N, Michel G, Lutz P, Neven B, Bertrand Y, Vannier JP, Ayas M, Matthes S, Elayoubi H, Devergie A, Kenzey C, Locatelli F, Peters C, Rocha V, Eapen M, Gluckman E. Hematopoietic Stem Cell Transplantation from HLA Identical Sibling Forsickle Cell Disease an International Survey on Behalf of Eurocord-Monacord, EBMT Paediatric Disease Working Party and CIBMTR. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL; Dec 5-8, 2015. Blood 126(23); 541. http://www.bloodjournal.org/content/126/23/541.abstract..
  • Cavazzana M, Ribeil J-A, Payen E, Suarez F, Beuzard Y, Touzot F, Cavallesco R, Lefrere F, Chretien S, Bourget P, Monpoux F, Pondarre C, Neven B, Schmidt M, von Kalle C, Kuypers FA, Sandler L, Soni S, Hermine O, Blanche S, De Montalembert M, Hacien-Bey-Abina S, Leboulch P. Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta AT87Q-Globin Vector. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 202. http://www.bloodjournal.org/content/126/23/202.abstract..
  • Dowling MM, Ramaciotti C, Kanter J, Osunkwo I, Inusa B, Lyer R, Kwiatkovvski J, Johnson C, Rhodes MM, Owen W, Strouse JJ, Quinn C, Panepinto JA, Neumayr L, Sarnaik S, Hynan LS, Plumb P, Kirkham F. Increased Prevalence of Potential Right-to-Left Shunting in Children with Sickle Cell Anemia and Stroke. American-Heart-Association/American Stroke Association International Stroke Conference. Nashville, TN; Feb 11-13, 2015. Stroke 2015;46. Link.
  • Field JJ, Majerus EM, Ataga KI, Vichinsky EP, Eaton C, Mazanet R, Nathan DG. NKTT120 Safely Depletes iNKT Cells in Stable Adult Sickle Cell Patients in a Phase 1 Trial. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 2178. http://www.bloodjournal.org/content/126/23/2178.abstract..
  • Fung EB, Luo G, Gildengoren G, Lal A. Effect of iron chelators on bone health in patients with thalassemia. 7th International Conference on Children's Bone Health. Salzburg, Austria; June 27-30, 2015. Link.
  • Gilbert S, Scott E, Thomas L, Boudreaux J, Quarmyne M, Carrion V, Kwiatkovvski J, Beatty J, Batts A, Thompson A, Welty S, Vichinsky E, Sayani, F., Russell E, Eile J, Neufeld E, Carson S, Lahat M, Coates T, Sayers S, Butler C, Cioffi G. Patient Outreach Methods Used to Locate Patients with Thalassemia in the United States. Tenth Cooley's Anemia Symposium. Chicago, IL; Oct 18 - 22, 2015. Poster #18 Link.
  • Heeney M, George A, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E. Clinical outcomes in pediatric and adult patients with sickle cell disease: Results of a 3-year, prospective, longitudinal noninterventional registry study. SCDAA 43rd Annual Convention; Sept 23-26, 2015. Baltimore, MD.
  • Heeney M, George A, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E. Clinical outcomes in pediatric and adult patients with sickle cell disease: Results of a 3-year, prospective, longitudinal noninterventional registry study. Association of Pediatric Hematology/Oncology Nurses. Providence, RI; Sept 17-19, 2015
  • Hoppe C. Controversies in Managing Sickle Cell Disease: NCAA vs AAP vs NIH Recommendations. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.305-312. University of California, San Francisco, School of Medicine.
  • Hoppe CC, Jacob E, Kuypers FA, Styles L. Simvastatin Reduces Frequency of Vaso-Occlusive Pain in Sickle Cell Disease: A Pilot Efficacy Trial. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 545. http://www.bloodjournal.org/content/126/23/545.abstract.
  • Kanter J, Walters MC, Hsieh M, Thompson AA, Krishnamurti L, Kwiatkowski J, Kamble RT, von Kalle C, Kuypers FA, Cavazzana M, Leboulch P, Sandler L, Soni S, Tisdale JF. Initial Results from Study Hgb-206: A Phase 1 Study Evaluating Gene Therapy By Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo with the Lentiglobin BB305 Lentiviral Vector in Subjects with Severe Sickle Cell Disease. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 3233. http://www.bloodjournal.org/content/126/23/3233.abstract.
  • Kaur R, Fung EB. Nutritional Attitudes and Beliefs Held by Patients with Thalassemia. Tenth Cooley's Anemia Symposium. Chicago, IL; Oct 18 - 22, 2015. Poster #17 Link.
  • Khurana M, Fung EB, Vichinsky E, Theil EC. Dietary Iron in Thalassemia: A New Look at Old Ideas. Tenth Cooley's Anemia Symposium. Chicago, IL; Oct 18 - 22, 2015. Poster #17 Link.
  • Kelly S, Marsh A, Quirolo K, Fink D, Garcia A, Weyhmiller M, Vichinsky E, Neumayr L. Comparison of transfusion adverse events in sickle cell disease patients receiving simple transfusions or automated red cell exchange for stroke prevention. American Society for Apheresis 36th Annual Meeting. San Antonio, TX; May 6-9, 2015. J Clin Apher 30(2); O-16. Link.
  • Kesselheim J, Bhatia N, Cronin A, Collaborative Group of Fellowship Program Directors. Measuring pediatric hematology-oncology fellows’ skills in humanism and professionalism: a novel assessment instrument. ASPHO 28th Annual Meeting. Phoenix, AZ; May 6-9, 2015. Poster #518. Link.
  • Krishnamurti L, Sullivan KM, Kamani NR, Waller EK, Abraham A, Campigotto F, Zhang W, Smith S, Hassell KL, Decastro L, Wu CJ, Neuberg DS, Walters MC. Results of a Multicenter Pilot Investigation of Bone Marrow Transplantation in Adults with Sickle Cell Disease (STRIDE). 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 543. http://www.bloodjournal.org/content/126/23/543.abstract.
  • Kutny MA, Alonzo TA, Gerbing RB, Wang Y-C, Fu C, Meshinchi S, Gamis AS, Feusner JH, Gregory J. Results of a Phase III Trial Including Arsenic Trioxide Consolidation for Pediatric Patients with Acute Promyelocytic Leukemia (APL): A Report from the Children's Oncology Group Study AAML0631. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL; Dec 5-8, 2015. Blood 126(23); 219. http://www.bloodjournal.org/content/126/23/219.abstract.
  • Lal A. Alpha Thalassemia Hb H Disease: An Emerging Public Health Problem. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.297-303. University of California, San Francisco, School of Medicine.
  • Lalefar NR, Hagar W. A Comparison of Hematologic Parameters in Patients with Sickle Cell Disease Undergoing Red Cell Exchange Using Terumo BCT Spectra Optia and COBE Spectra Apheresis Systems. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 4743. http://www.bloodjournal.org/content/126/23/4743.abstract.
  • Lalefar NR, Walters MC. Graft Failure after Hematopoietic Cell Transplantation for Hemoglobin Disorders: Successful Application of a Rescue Regimen. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 5460. http://www.bloodjournal.org/content/126/23/5460.abstract.
  • Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris C. Are we missing the mark? Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest syndrome (ACS). Pediatric Academy Society Annual Meeting. San Diego, CA; April 2015.
  • MacKenzie T, Walters M, Vichinsky E. In utero transplantation in patients with Alpha Thalassemia Major: the birth of a new therapy. Second International Conference on In Utero Transplantation and Fetal Gene Therapy. London, England; October 9-30, 2015.
  • MacKenzie T, Walters M, Vichinsky E. In utero transplantation in patients with Alpha Thalassemia Major: the birth of a new therapy. Tenth Cooley's Anemia Symposium. Chicago, IL; October 18-22, 2015. Poster #27. Link.
  • Minkley M, Praschberger M, Jackson A, Smith D, Sweeters N, Borchers C, Vichinsky E, Macleod P, Walter P. Systemic plasma biomarkers as a tool to help assess the efficacy of NBIA clinical trials; results from a pilot trial of deferiprone chelation to treat a case of PARK14 Parkinsonism/PLA2G6 associated neurodegeneration (PLAN). 19th International Congress of Parkinson's Disease and Movement Disorders. San Diego, CA; June 14-18, 2015. Movement Disorders 2015;30 Suppl 1 :271. Link.
  • Paulukonis S, Hagar RW. California's RuSH Sickle Cell Disease Cohort: Emergency Department Utilization 2005-2013. 9th Annual Sickle Cell Disease Research and Educational Symposium and 38th National Sickle Cell Disease Scientific Meeting. Hollywood, FL; April 10-13, 2015. Foundation for Sickle Cell Disease Research, poster #JSCDH-D-15-00075.
  • Puri L, Matsunaga A. Idiopathic hypereosinophilic syndrome with cardiac thrombus in a four year old girl: a case reportand review of the literature. American Society of Pediatric Hematology/Oncology 28th Annual Meeting. Phoeniz, AZ; May 6-9, 2015. Pedatr Blood & Cancer 62(S1); 629.
  • Rai P. Idiopathic hypereosinophilic syndrome with cardiac thrombus in a four year old girl: a case reportand review of the literature. Scientific Symposium of the Hemostasis and Thrombosis Research Society (HTRS). New Orleans, LA; April 16-18, 2015. Poster.
  • Rai P, Winstead M, Feusner J. Cerebral metastasis of hepatoblastoma: what is the best therapy? American Society of Pediatric Hematology/Oncology 28th Annual Meeting. Phoeniz, AZ; May 6-9, 2015. Pedatr Blood & Cancer 62(S1); 661. .Link.
  • Rai P, Matsunaga A. Superior sagittal sinus thrombus, a presenting feature of Paroxysmal Nocturnal Hemoglobinuria in a fifteen year old female: A case report and literature review. Scientific Symposium of the Hemostasis and Thrombosis Research Society (HTRS). New Orleans, LA; April 2015.
  • Shenoy S, Eapen M, Wu J, Walters MC, Levine JE, Logan B, Gersten ID, Kamani NR. A Multicenter Phase II Trial of Unrelated Donor Reduced Intensity Bone Marrow Transplantation for Children with Severe Sickle Cell Disease (SCURT): Results of the Blood and Marrow Transplant Clinical Trials Network (BMT CTN 0601) Study. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL; Dec 5-8, 2015. Blood 126(23); 619. http://www.bloodjournal.org/content/126/23/619.abstract.
  • Sloan JS, Agrawal AK, Alisanski S. Establishment of a National Paediatric Haematology-Oncology Program in Botswana. 48th Congress of the International Society of Paediatric Oncology. Capetown, South Africa; Oct 8-11, 2015.
  • Smith WR, McClish DI, Lottenberg R, Chen I, Villela, Sisler I, Johnson S, Trice D, Sop D, Keller S, Treadwell M, Haywood C. Patient reported outcomes in sickle cell disease: current results from PROMIS, ASCQ-ME, & utility in clinical trials. NHLBI Annual Sickle Cell Disease Clinical Trials Meetings; Aug 18-22, 2015. Bethesda, MD.
  • Vichinsky E, Kwiatkowski J, Giardina P, Paley C, Vekeman F, Cheng W, Damron J, McCormick N, Sasane M, Qui Y, Sheng DM, Thompson A. Epidemiologic and clinical characteristics of thalassemia intermedia in the United States. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 3279. http://www.bloodjournal.org/content/126/23/3279.
  • Walter PB, Hohman L, Rokeby A, Lum J, Hagar R, Stewart M, Lavrisha L, Vichinsky E, Morris CR. The Effects of Glutamine Supplementation on Markers of Autophagy and Apoptosis in Peripheral Blood Mononuclear Cells from Patients with Sickle Cell Disease. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 3412. http://www.bloodjournal.org/content/126/23/3412.abstract.
  • Walter PB, Slater N, Harmatz P, Higa A, Ng V, Weyhmiller M, Evans P, Porter JB, Sweeters N, Price J, Killilea D, Neumayr L, Lal A, Vichinsky E. Iron Level and Monocyte Morphology Predict TLR4 Expression and Reactive Oxygen Species Production Which Influences Chronic Inflammation in ß-Thalassemia. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL; Dec 5-8, 2015. Blood 126(23); 950. http://www.bloodjournal.org/content/126/23/950.abstract.
  • Walters MC, Rasko J, Hongeng S, Kwiatkowski J, Schiller GJ, Kletzel M, Ho PJ, Vichinsky E, von Kalle C, Cavazzana M, Leboulch P, Petrusich A, Soni S, Thompson AA. Update of Results from the Northstar Study (HGB-204): A Phase 1/2 Study of Gene Therapy for Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex-Vivo with a Lentiviral Beta AT87Q-Globin Vector (LentiGlobin BB305…. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 201. http://www.bloodjournal.org/content/126/23/201.abstract.
  • Winstead M, Walters M. Immunologic reconstitution in patient receiving hematopoietic stem cell transplantation for hemoglobin disorders: single-institution experience. Poster, ASPHO 28th Annual Meeting. Phoenix, AZ; May 6-9, 2015.

2014:

  • Abikoff CM, Talano J-A, Keever-Taylor CA, Walters MC, Shenoy S, Moore T, Parsons SK, Dozor AJ, Friedman D, Chitti R, Shi Q, Grossman BJ, Weinberg RS, Morris E, Brand P, Foley S, Militano O, Ayello J, Semidei-Pomales M, Baxter-Lowe LA, Cairo MS. Familial Haploidentical (FHI) T-Cell Depleted (TCD) with T-Cell Addback Stem Cell Transplantation for Patients with High-Risk Sickle Cell Disease (SCD) (IND 14359). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2582. http://www.bloodjournal.org/content/124/21/2582.
  • Adams-Graves P, Heeney M, Mueller B, Baltz B, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E. Treatment patterns and clinical outcomes among patients with sickle cell disease: 24-month follow-up on a 3-year, prospective, non-interventional registry. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014. Pediatric Blood & Cancer. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
  • Adisa F, Buchanan I, Morris CR. BiPap use in children with sickle cell disease (SCD) and acute chest syndrome (ACS). 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 2014.
  • Akinsola B, Hagbom R, Zmitrovich A, Kavanagh P, Ashkouti A, Fletcher A, Vinson N, Simon HK, Fleming A, Jain S, Adisa O, Dampier C, Morris CR. Adding intranasal fentanyl (INF) to the management of sickle cell disease (SCD) vaso-occlusive pain episodes (VOE) at a pediatric emergency department (ED): a quality improvement study. 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 2014.
  • Akinsola B, Hagbom R, Zmitrovich A, Kavanagh P, Ashkouti A, Fletcher A, Vinson N, Simon HK, Fleming A, Jain S, Adisa O, Dampier C, Morris CR. More rapid delivery of parenteral analgesia by adding intranasal fentanyl to the management of sickle cell disease vaso-occlusive pain episodes at a pediatric emergency department. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).
  • Badawy SM, Pinckney K, Meier ER, Myers K, Black V, Hastings CA, Hilden J, Zweidler-McKay PA, Stork L, Vaiselbuh SR, Johnson TS. First interim analysis of the ASPHO mentoring program. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
  • Fung EB, Killilea DW, Shenvi S, Haines D, Lavrisha L, Flores B, Higa A, Ahmad T, Lal A. Marginal zinc status associated with altered insulin metabolism in patients with thalassemia. 4th International Society for Zinc Biology Meeting. Asilomar, CA; Sep 14-19, 2014. poster presentation, abstract #FF10.
  • Fung EB, Sushrita N, Haines D, Schroepfer C, Lal A. Dietary Intake Insufficient to Support Nutritional Adequacy in Patients with Thalassemia. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 1361. http://www.bloodjournal.org/content/124/21/1361.
  • Hacker NA, King JC, Van Loan MD, Gertz ER, Adams M, Sawyer A, Fung EB. Calcium supplementation during pregnancy improves tibial bone density at one year post-partum in racially diverse women. Experimental Biology Conference, April 2014. San Diego, CA. #14-7168.
  • Heeney MM, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E, George A. Comparison of Clinical Outcomes Between Adult and Pediatric Patients (pts) with Sickle Cell Disease (SCD): 3-Year (y) Follow-up in a Prospective, Longitudinal, Noninterventional Registry Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4890-. http://www.bloodjournal.org/content/124/21/4890.
  • Keller SD, Treadwell MJ, Yang M, Werner EM, Hassell KL. Patient reports of health outcomes in sickle cell disease: psychometric properties of the Adult Sickle Cell Quality of Life Measurement System. 2nd Global Congress on Sickle Cell Disease. Rio de Janiero, Brazil: November 11-14, 2014. http://www.hemorio.rj.gov.br/CongressoGSCDN/programa.pdf.
  • Khurana M, Vichinsky E, Theil EC. Efficacy of clinical iron chelators varies in iron-overloaded liver cells. 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 11-14, 2014. Poster presentation.
  • Khurana M, Kanathezhath B, Feusner J. Recurrent/refractory metastatic osteosarcoma responds to TRAIL therapy. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
  • Khurana M, Vichinsky E, Theil EC. Head-to-head comparison of current clinical iron chelators on cellular ferritin regulation in HEPG2 cell culture model. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
  • Klaasen R, N. B, Merelles-Pulcini M, Vichinsky E, Kirby-Allen MN, E., Kwiatkovvski J, Wu J, Blanchette, V., Young N. Validation of the TranQol Parental Burden Measure: a new tool for parents of children with thalassemia major. 21st Annual Conference of the International Society for Quality of Life Research. Berlin, Germany; Oct 15-18, 2014. Poster presentation. Link.
  • Kutny MA, Alonzo TA, Gerbing RB, Wang Y-C, Fu C, Meshinchi S, Gamis AS, Feusner JH, Gregory J. Arsenic Trioxide Is a Well Tolerated Consolidation Regimen in Children with Newly Diagnosed Acute Promyelocytic Leukemia; Toxicity Results of the Children's Oncology Group AAML0631 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 985-. http://www.bloodjournal.org/content/124/21/985.
  • Kutny MA, Geyer S, Laumann KM, Gregory J, Willman CL, Stock W, Larson RA, Powell BL, Feusner JH. A Comparison of Outcomes Between Adolescents and Young Adults (AYA) and Children with Acute Promyelocytic Leukemia (APL): North American Intergroup Study CALGB 9710 (Alliance). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2306-. http://www.bloodjournal.org/content/124/21/2306.
  • Kutny MA, Geyer S, Laumann KM, Gregory J, Willman CL, Stock W, Larson RA, Powell BL, Feusner JH. Effect of Young Age on Outcomes in Pediatric Acute Promyelocytic Leukemia (APL): North American Intergroup Study CALGB 9710 (Alliance). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2301-. http://www.bloodjournal.org/content/124/21/2301.
  • Kutny MA, Rajpurkar M, Alonzo TA, Gerbing RB, Gamis AS, Feusner JH, Gregory J. Evaluation of ISTH DIC Score to Predict Significant Bleeding and Thrombosis Events in Pediatric Acute Promyelocytic Leukemia; A Report from the Children's Oncology Group AAML0631 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 3669-. http://www.bloodjournal.org/content/124/21/3669.
  • Lal A, Patterson L, Goldrich A, Marsh A, Yen K, Bhatnagar A. Detection of elevated end-tidal carbon monoxide concentration in children with sickle cell anemia. PAS/ASPR Joint Meeting. Vancouver, Canada: May 3-6, 2014. Pediatric Academic Societies and Asian Society for Pediatric Research.
  • Lal A, Yen K, Patterson L, Goldrich A, Marsh AM, Bhatnagar A. Elevated End-Tidal Carbon Monoxide Concentration in Children with Sickle Cell Anemia. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 1390-. http://www.bloodjournal.org/content/124/21/1390.
  • Lalefar NR, Walters M. Graft failure after hematopoietic cell transplantation for hemoglobionpathies; successful rescue with alternate donors. Annual Sickle Cell Disease Research and Educational Symposium and 37th National Sickle Cell Disease Scientific Meeting. Miami, FL; April 11-14, 2014.
  • Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris CR. Are we missing the mark? Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest syndrome (ACS). 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 2014.
  • Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris CR. Are we missing the mark? Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest syndrome (ACS). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).
  • Lee JH, Rademaker AW, Powell BL, Geyer S, Larson RA, Gregory J, Hijiya N, Feusner JH. Obesity Does Not Affect the Recurrence Free Survival Rates in Children Less Than 20 Years of Age in Acute Promyelocytic Leukemia (APL). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 957. http://www.bloodjournal.org/content/124/21/957.
  • Lew G, Lu X, Yanofsky R, Rheingold SR, Whitlock J, An Q, Devidas M, Hastings CA, Winick NJ, Carroll WL, Borowitz MJ, Hunger S, Pulsipher MA. Outcomes after Intermediate-Risk Relapse of Childhood B-Lymphoblastic Leukemia (B-ALL) and the Role of Allogeneic Stem Cell Transplantation (SCT): A Report from Children's Oncology Group (COG) AALL0433. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 684. http://www.bloodjournal.org/content/124/21/684.
  • Lew G, Lu X, Yanofsky RA, Rheingold SR, Whitlock JA, Gulig SD, Devidas M, Pulsipher MA, Hastings CA, Winick NJ, Carroll WL, Borowitz MJ, Hunger SP. The significance of minimal residual disease (MRD) in relapsed childhood B-lymphoblastic leukemia: Interim analysis of Children's Oncology Group (COG) protocol AALL0433. ASCO Annual Meeting. Chicago, IL; May 30-June 3, 2014. J Clin Oncol 32:5s(2014 suppl ); abstr 10014.
  • Majerus EM, Ataga KI, Vichinsky E, Eaton CA, Mazanet R, Nathan DG, Field JJ. NKTT120 Reduces iNKT Cells without Dose Limiting Toxicity in Stable Adult Sickle Cell Patients in a Phase 1 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2718. http://www.bloodjournal.org/content/124/21/2718.
  • Minkley M, Praschberger M, Jackson A, Smith D, Sweeters N, Borchers C, Vichinsky E, Macleod P, Walter P. Validation of the TranQol Parental Burden Measure: a new tool for parents of children with thalassemia major. 18th International Congress of Parkinson's Disease and Movement Disorders. Stockholm, Sweden; Oct 15-18, 2014. Movement Disorders 2015;30 Suppl 1:271. Link.
  • Minkley M, Praschberger M, Jackson A, Smith D, Sweeters N, Borchers C, Vichinsky E, MacLeod P, Walter PB. Multiplex Multiple Reaction Monitoring (MRM) Proteomic Investigation Reveals Altered Iron Trafficking and Elevated Systemic Oxidative Stress (OS) and Inflammatory Biomarkers in a Patient with Neurodegeneration with Brain Iron Accumulation (NBIA). Society for Free Radical Biology and Medicine Annual Meeting, (SFRBM 2014) Volume: 76, S1. Seattle, WA; 2014.
  • Minkley M, Praschberger M, Jackson A, Smith D, Borchers C, Macleod P, Walter PB. A pilot investigation of systemic iron trafficking, oxidative stress and inflammation in a case of PLA2G6 associated (PARK14) neurodegeneration with brain iron accumulation (NBIA) undergoing deferiprone treament. 18th International Congress of Parkinson's Disease and Movement Disorders. Stockholm, Sweden; June 8-12, 2014. Movement Disorders 2014;29 Suppl 1 :675. Link.
  • Morris C, Latronica C, Kuypers FA, Rosenfeld H, Larkin SK, Doniger S, Vichinsky E, Shiva S. Citrate Synthase Activity Is Increased In Children With Sickle Cell Disease (SCD) On Hydroxyurea (HU) Therapy. 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 2014.
  • Neumayr L. Neuropsychological dysfunction and neuroimaging abnormalities in neurologically intact adults with sickle cell anemia. 8th Annual Sickle Cell and Thalassemia Advanced Conference. London, U.K.; October 1-3, 2014.
  • Neumayr L, Karin I, Sweeters N, Buchner B, Giambusso K, Ferguson J, Zorzi G, Blamire A, Baur A, Hayflick S, Hogarth P, N. F, Klucken A, Jaskolka H, Wood P, Gauzy F, Tricta F, Fradette C, Lee J, Tran L, Kmiec T, Chinnery P, H. S, Nardocci N, Zibordi F, Vichinsky E, Klopstock T, Spino M. Journey of a rare disease: an 18-month review of the complex logistics in a Phase III international trial of neurodegenerative brain iron accumulation (NBIA). TIRCON General Assembly Meeting. Stressa, Italy; October 2014.
  • Paulukonis S, Currier R, Coates TD, Vichinsky E, Feuchtbaum L. Impact of Immigration and Migration on Thalassemia Surveillance in California, 2004-2008. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4855-. http://www.bloodjournal.org/content/124/21/4855.
  • Paulukonis S, Griffin T, Zhou M, Eckman JR, Hagar R, Bauer Snyder A, Feuchtbaum L, Grant AM, Hulihan M. Sickle Cell Disease Mortality in California and Georgia 2004-2008. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 439-. http://www.bloodjournal.org/content/124/21/439.
  • Praschberger M, Minkley M, Jackson A, Smith D, Borchers C, Vichinsky E, MacLeod P, Walter PB. Using Proteomics To Assess Potential Biomarkers Of Systemic Iron Trafficking, Inflammation And Oxidative Stress In A Patient With PLA2G6 Associated Neurodegeneration (PLAN) Being Treated With Deferiprone. 18th International Congress of Parkinson's Disease and Movement Disorders. Stockholm, Sweden; Oct 15-18, 2014. Movement Disorders 2015;30 Suppl 1:76. Link.
  • Puri L. Role of a sphingolipid regulated novel oncogene in pediatric malignancies. CHORI Research Symposium. Children’s Hospital & Research Center Oakland, CA; Sept 26, 2014.
  • Singer ST, Wang J, Yuan Q, Vichinsky E, Smith J, Paley C, Fischer R. Pituitary Iron and Volume Are Affecting Hormones and Reproductive Potential. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4048. https://ash.confex.com/ash/2014/webprogram/Paper75574.html.
  • Slater NR, Harmatz P, Higa A, Ng V, Weyhmiller M, Evans P, Porter JB, Sweeters N, Price J, Manji A, Manocha A, Killilea DW, Lal A, Neumayr L, Vichinsky E, Walter PB. Iron Overload and Hemolysis Modulate Monocytes and Inflammation in Beta-Thalassemia. Society for Free Radical Biology and Medicine (SFRBM) Annual Meeting. Seattle, WA 2014; 76(S65-S).
  • Thompson AA, Rasko JE, Hongeng S, Kwiatkowski JL, Schiller G, von Kalle C, Cavazzana M, Leboulch P, Petrusich A, Soni S, Walters MC. Initial Results from the Northstar Study (HGB-204): A Phase 1/2 Study of Gene Therapy for ?-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral ??-T87Q -Globin Vector (LentiGlobin BB305 Drug Product). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 549. Nominated for Best of ASH abstract. http://www.bloodjournal.org/content/124/21/549.
  • Treadwell M, Paulukonis S, Currier B, Hutchinson C, Neumayr L, Vichinsky E, Feuchtbaum L. Population-based study of mental health diagnoses and utilization in sickle cell disease. Annual Sickle Cell Disease Research and Educational Symposium and 37th National Sickle Cell Disease Scientific Meeting. Miami, FL; April 11-14, 2014. Poster presentation.
  • Treadwell M, Johnson S, Sisler I, Gildengorin G, Medina R, Barreda F, Bitsko M, Smith WR. Evaluation of a sickle cell disease specific readiness for transition assessment. 8th Annual Sickle Cell Disease Research & Educational Symposium and 37th National Sickle Cell Disease Scientific Meeting. Miami, FL. April 11-14, 2014. Journal of Sickle Cell Disease and Hemoglobinopathies 2014(1; doi 10.14223/JSCDH-D-14-00081).
  • Vichinsky E, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, George A, Heeney MM. Clinical complications in pediatric and adult sickle cell disease. Association of Pediatric Hematology/Oncology Nurses (APHON) Annual Conference & Exhibit. Portland, OR; Sep 4-6 2014. poster presentation.
  • Walter PB, Hohman L, Rokeby A, Manocha A, Lum JJ, Lavrisha L, Stewart M, Hagar R, Vichinsky E, Morris CR. The effects of glutamine supplementation on markers of autophagy and apoptosis in peripheral blood mononuclear cells from patients with sickle cell disease. Free Radical Biology and Medicine. Seattle, WA; Nov 2014.
  • Walter PB, Hohman L, Rokeby A, Manocha A, Lum JJ, Lavrisha L, Stewart M, Hagar R, Vichinsky E, Morris CR. The effects of glutamine supplementation on markers of autophagy and apoptosis in peripheral blood mononuclear cells from patients with sickle cell disease. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).
  • Walter PB, Otto S, Sharf K, Riddett E, Tan HH, Fournier R, Zhang F, Choy F, Linhardt R, Lum JJ, Harmatz P. Investigation of pharmacological chaperones and glutathione in the enhancement of N-acetylgalactosamine-6-sulfate sulfatase (GALNS) in the treatment of mucopolysaccharidosis IVA. Society for Free Radical Biology and Medicine (SFRBM) Annual Meeting; 76(S1), #224. Seattle, WA; Nov 2014.
  • Wun T, Telen MJ, Krishnamurti L, McCavit TL, DeCastro LM, Flanner H, Kuypers FA, Larkin SK, Rhee S, Magnani JL, Thackray HM. Pan-Selectin Antagonist Rivipansel (GMI-1070) Reduces Soluble E-Selectin Levels While Improving Clinical Outcomes in SCD Vaso-Occlusive Crisis. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2704. http://www.bloodjournal.org/content/124/21/2704.
  • Yang E, Heeney M, Baltz B, Adams-Graves P, Paley C, Esposito J, McNamara K, Vichinsky E, George A. 24-month follow-up for treatment patterns and clinical outomes among patients with sickle cell disease in an ongoing 3-year prospective, non-interventional registry. 42nd Annual SCDAA National Convention. Baltimore, MD; Oct 1-4, 2014. Poster presentation.

The following sections are not yet complete and include only a small portion of our lectures, presentations and honors..


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Invited Lectures:

2016

  • Agrawal A. Invited Talk. American College of Veterinary Internal Medicine, Special Symposium, Oncology.
  • Treadwell MJ. Invited Talk, Sickle Cell Disease Ontology Meeting. Pan African Bioinformatics Network for Human Heredity and Health in Africa (H3 Africa), Cape Town, South Africa.
  • Treadwell MJ. Invited presentations, panel; Indiana Sickle Cell Conference. Indiana University School of Medicine, Indianapolis, IN.
  • Vichinsky E. Hematopoietic Stem Cell Transplantation is NOT Standard of Care for Secondary Prevention of Cerebrovascular Infarcts in Sickle Cell Disease Sickle Cell in Focus Conference; presentation and debate; June 2-3, 2016; National Institutes of Health, Bethesda, MD.
  • Walters M. Invited Presentation. Kiadis Meeting, Amsterdam, Netherlands.
  • Walters M. Invited Presentation. CBBS Meeting, San Diego, CA.
  • Walters M. Invited Presentation. SCD Meeting, Hollywood, FL.
  • Walters M. Invited Presentation. ASPHO LTFU Conference, Minneapolis, MN.

2015:

  • Fung EB. Bone and Nutritional Considerations in Thalassemia. Lifelines Conference; Sept 25, 2015, Thalassemia Foundation of Canada.
  • Fung EB. Endocrine Blast. Lifelines Conference; Sept 26, 2015, Thalassemia Foundation of Canada.
  • Fung EB. Importance of Nutrition for Health in Patients with Thalassemia. Cooley's 10th Anniversary Meeting, Chicago IL; Oct 19-22, 2015, NY Academy of Science.
  • Hoppe C. Genetic determinants of Clinical Outcomes in Sickle Cell Disease. RBC-Omics, Red Cell Genetics Analysis Advisory Group; March 24, 2015; National Heart, Lung and Blood Institute, Bethesda, MD.
  • Hoppe C. Controversies in Managing Sickle Cell Disease: NCAA vs AAP vs NIH Recommendations. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.305-312. University of California, San Francisco, School of Medicine.
  • Hoppe C. Limitations of Transfusion Therapy for Cerebral Infarcts in Sickle Cell Disease and Future Directions. AABB Annual meetings. Anaheim, CA; October 24-27, 2015.
  • Hoppe C. Newborn Screening and Point-of-Care Testing in Developing Countries 10th Sickle Cell in Focus Conference. NIH, Bethesda MD, June 2-3, 2016.
  • Hoppe C. Neonatal Red Blood Cell Disorders: Abnormal Neonatal Screening to Symptomatic Anemia. AAP National Meetings, San Francisco, CA, October 24-25, 2016.
  • Lal A. Alpha Thalassemia Hb H Disease: An Emerging Public Health Problem. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.297-303. University of California, San Francisco, School of Medicine.
  • Matsunaga A. ITP Management Dilemmas. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.249-260. University of California, San Francisco, School of Medicine.
  • Treadwell MJ. Invited Talk, Community Engagement Workshop. H3 Africa Consortium Meeting, Livingstone, Zambia.
  • Treadwell M. Neurocognitive Issues in Sickle Cell Disease. West Coast Sickle Cell Nurses Annual Meeting; Sept 28, 2015, Los Angeles, CA.
  • Treadwell M. Person and Family Centered Outcomes. Clinical Data Research Network Annual Meeting; Mar 15-16, 2015; Vanderbilt-Meharry Center of Excellence in Sickle Cell Disease, Mid-South Clinical Data Research Network, Nashville, TN.
  • Treadwell M. Quality of Life and Quality of Care in Adults with Sickle Cell Disease. 9th Annual Sickle Cell and Thalassaemia Advanced Conference; Oct 7-9, 2015; Guys & St. Thomas' NIH Foundation Trust, London, U.K.
  • Treadwell M. Sickle Cell Disease and Access to Care: a National Crisis. Annual Conference of the National Medical Association, Region IV; May 28, 2015.
  • Treadwell M. Sickle Cell Disease: Impact on Individuals and Families. Gene Editing and a Path to a Cure for Sickle Cell Disease; July 28, 2015; Congressional Briefing sponsored by the Sickle Cell Disease Association of America, the Congressional Sickle Cell Caucus and the Research and Development Caucus, Washington, D.C.
  • Treadwell M, Hodge J. Disparities in African American Health: Sickle Cell Disease. Mar 5, 2015; Office of Diversity and Inclusion, Samuel Merritt University, Oakland, CA.
  • Treadwell M, Murphy W, Johnson T, Lal A. Self-Efficacy and Adherence with Iron Chelation Therapies: Motivational Interviewing Interventions. Tenth Cooley's Anemia Symposium; Oct 18-22, 2015, Chicago, IL.
  • Treadwell M, Vichinsky E, Nugent D. Pacific Sickle Cell Regional Collaborative. Sickle Cell Disease Association of America 43rd Annual Convention; Sep 23-26, 2015, Baltimore, MD.
  • Treadwell M. Charles Whitten Memorial Lecture. Sickle Cell Disease Association of America 43rd Annual Convention; Sep 23-26, 2015, Baltimore, MD.
  • Vichinsky E. Iron Deficiency & Iron Metabolism Disorders: More Serious and Common Than You Think. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.261-270. University of California, San Francisco, School of Medicine.
  • Vichinsky E. Diagnosis and Management of Iron Overload. ASH Consultative Hematology Course; Dec 7, 2015; American Society of Hematology, Orlando, FL; http://www.hematology.org/Annual-Meeting/Program/CHC.aspx.
  • Vichinsky E. Diagnosis and Management of Iron Overload. ASH Consultative Hematology Course; Sept 17, 2015; American Society of Hematology, Chicago, IL; http://www.hematology.org/Meetings/CHC/4010.aspx.
  • Vichinsky E. Sickle Cell Disease: Update on Emerging Therapies. Research in Progress Seminar; Feb 27, 2015; UCSF School of Medicine, San Francisco, CA.
  • Walters M. Invited Presentation. SCD Research Meeting, Hollywood, FL.
  • Walters M. Invited Presentation. SCDAA Meeting, Baltimore, MD.
  • Walters M. Invited Presentation. Cooley's Anemia Meeting, Orlando, FL.
  • Walters M. Invited Presentation. ASH Annual Meeting, Orlando, FL.
  • Walters M. Invited Presentation. Umbilical Cord Blood Meeting, Monaco.
  • Walters M. Invited Presentation. Iron Meeting, Berlin, Germany.
  • Walters M. Invited Presentation. ASBMT Meeting, San Diego, CA.

2014:

  • Hoppe C. Statins in Sickle Cell Disease. DDCF ICRA Breakthroughs in Sickle Cell Disease Research Workshop; Sept 22, 2014, New York, NY.
  • Hoppe C. Clinical trial highlights in sickle cell disease. 8th Annual Sickle Cell in Focus Conference; Sept 15, 2014; National Heart, Lung and Blood Institute, Bethesda, MD.
  • Hoppe C. Newborn screening for Hemoglobinopathies. Advanced Workshop on Sickle Cell Disease; Oct 24, 2014; UCSF Benioff Children's Hospital Oakland, Oakland, CA.
  • Lal A. Thalassemia Intermedia. UC Davis, Dept of Pediatrics, Grand Rounds; Feb 3, 2014; Davis, CA.
  • Lal A. Iron Chelation Therapy. Thalassemia Patient and Family Conference, Jan 18, 2014, UCSF Benioff Children's Hospital Oakland, Oakland, CA. http://www.thalassemia.com/2014-patient-family-conference.aspx.
  • Levine L. Progress. "Evening Under the Stars", May 3, 2014, Oakland CA. https://www.youtube.com/watch?v=UF5EeH01CNs.
  • Treadwell MJ. Plenary talk and workshop organizer. Global Congress on Sickle Cell Disease, Rio de Janeiro, Brazil.
  • Treadwell MJ. Invited talk, Sickle Cell Disease Workshop. H3 Africa Consortium Meeting, Dar es Salaam, Tanzania.
  • Treadwell MJ. Sickle cell disease - the role of the school nurse. Ethnic Health Institute Annual Nurses Training; January 2014, Oakland, CA.
  • Treadwell MJ. Determinants of quality of life in the thalassemias. Annual Conference, Guys and St Thomas NHS Foundation Trust; October 2014, London, U.K
  • Treadwell MJ, Peyton W. Sickle Cell Disease: Myths and Realities. Family Voices of California; August 2014, Oakland, CA.
  • Vichinsky E. The Complex Pathophysiology of the Hemoglobinopathies: Guiding Us to Innovative Challenges. Presidential Symposium; May 14-17, 2014, 27th Annual ASPHO Meeting, Chicago, IL.
  • Vichinsky E. Cerebrovascular disease in adult patients with sickle cell anemia. Sickle Cell in Focus Conference; Sept 15-16, 2014; National Institutes of Health, Bethesda, MD.
  • Vichinsky E, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, George A, Heeney MM. Clinical complications in pediatric and adult sickle cell disease. Association of Pediatric Hematology/Oncology Nurses (APHON) Annual Conference & Exhibit. Portland, OR; Sep 4-6 2014. poster presentation.
  • Vichinsky E. Thalassemia Research and Care Update. Thalassemia Patient and Family Conference, Jan 18, 2014, Oakland CA.
  • Walters M. Bone Marrow/Stem Cell Transplant/Gene Therapy. Thalassemia Patient and Family Conference, Jan 18, 2014, Oakland CA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. May 4, 2014; Berkeley Stem Cell Center, Berkeley, CA.
  • Walters MC. Thalassemia Debate. European Hematology Association 19th Congress; June 10-15, 2014, Milan, Italy.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. July 29-30, 2014, Children's Hospital Los Angeles, CA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. Sep 5, 2014; Fred Hutchinson Cancer Research Center, Seattle, WA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. DeCal lecture; Sep 29, 2014; University of California, Berkeley, CA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. UCSF Hematology/Oncology Division; Oct 27, 2014; University of California, San Francisco, CA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. UCSF/CHORI Translational Research Retreat; Oct 29, 2014; Oakland, CA.
  • Walters MC. Bone marrow transplantation and hematopoiesis. Nov 14, 2014; Bayer, San Francisco, CA.
  • Walters MC. Invited Presentation. ACBSCT Meeting, Rockville, MD.
  • Walters MC. Invited Presentation. American Society of Hematology Meeting, San Francisco, CA.
  • Walters MC. Invited Presentation. SCD Meeting, Miami, FL.
  • Walters MC. Invited Presentation.AABBUCB Symposium, San Francisco, CA.

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Presentations

2016

  • Agrawal A. Oncology Nursing Seminar; Children's Hospital Oakland, CA.
  • Agrawal A. Presentation. Pediatric Oncology Tumor Board; Children's Hospital Oakland, CA.
  • Agrawal A. Presentation. Pediatric Resident Noon Seminar; Children's Hospital Oakland, CA.
  • Rai P. Transfusion Medicine. April 2016; UCSF Benioff Children's Hospital Oakland, Oral faculty presentation educational conference.
  • Rai P. Exploring the role of SIRT3 in mitigating radiation therapy induced late bone marrow injury. June 4, 2016; Scholarship Oversight Committee, Children's Hospital Oakland Research Institute, Oakland CA.
  • Walters M. Presentation, BMT Nursing Program, Oakland, CA.
  • Winstead M. Respiratory physiology under hypoxic conditions in Berkeley sickle cell mice. Scholarship Oversight Committee, Children's Hospital Oakland Research Institute, Oakland CA. June 4, 2016.
  • Winstead M, Sun P, Martin K, Earl J, Neumayr L, Hoppe C, Vichinsky E. Enchephaloduroarteriosynangiosis (EDAS) in young patients with sickle cell disease: single-institution experience. Scholarship Oversight Committee, Children's Hospital Oakland Research Institute, Oakland CA. June 4, 2016,'

2015

  • Agrawal A. Presentation. Global Health Interest Group.
  • Agrawal A. Presentation. Pediatric Oncology Tumor Board; Children's Hospital Oakland, CA.
  • Agrawal A. Presentation. Hematology/Oncology Fellows Conference; Children's Hospital Oakland, CA.
  • Agrawal A. Presentation. Oncology Nursing Seminar; Children's Hospital Oakland, CA.
  • Agrawal A. Presentation. Pediatric Resident Noon Seminar; Children's Hospital Oakland, CA.
  • Agrawal A. Presentation. Global Health Symposium; University of California, San Francisco, CA.
  • Agrawal A. Presentation. Pediatric Oncology Tumor Board; Children's Hospital Oakland, CA.
  • Kelly S. Comparison of Transfusion Adverse Events in Children with Sickle Cell Disease (SCD) Receiving Simple or Automated Red Blood Cell Exchange (aRBX) Transfusions for Stroke Prevention. American Society for Apheresis 36th Annual Meeting, San Antonio, TX; May 6-9, 2015; Oral presentation. Link.
  • Lalefar N, Puri L. Where did all the platelets go? A look at Childhood Immune Thrombocytopenic Purpura. Grand Rounds; Apr 21, 2015, UCSF Benioff Children's Hospital Oakland, CA.
  • Quirolo K. Acute Chest Syndrome: Rationale for Red Blood Cell Exchange and/or Simple Transfusion. American Society for Apheresis 36th Annual Meeting, San Antonio, TX; May 6-9, 2015; oral presentation. Link.
  • Rai P. Acute Promyelocytic Leukemia. January 2015; UCSF Benioff Children's Hospital Oakland, Oral faculty presentation educational conference.
  • Rai P. Germ Cell Tumors. April 2015; UCSF Benioff Children's Hospital Oakland, Oral faculty presentation educational conference.
  • Rai P. Juvenile Myelomonocytic Leukemia. June 2015; UCSF Benioff Children's Hospital Oakland, Oral faculty presentation educational conference.
  • Rai P. Alpha Thalassemia. October 2015; UCSF Benioff Children's Hospital Oakland, Oral faculty presentation educational conference.
  • Singer ST. Alpha Thalassemia: Hemoglobin H, Hemoglobin H/Constant Spring and other subtypes. HRSA Centers for Thalassemia in the Western United States, Children's Hospital Oakland Research Institute; October 2015.
  • Walters M. SCA Transplant and Donor Pools. Samuel Merritt College RN Students, Oakland, CA.
  • Walters M. BMT RN Training (Overview and TBI). UCSF Benioff Children's Hospital Oakland, Oakland, CA.
  • Walters M. Talk, Berkeley Stem Cell Center Retreat, Asilomar, CA.
  • Walters M. Talk, CAR-T Consortium Meeting, Seattle, WA.
  • Walters M. Talk, SSSCR Conference UC Berkeley, CA.
  • Walters M. Talk, Pacific Sickle Cell Regional Collaborative, Oakland, CA.
  • Weyhmiller M. SQUID Demonstration. Pacific Sickle Cell Regional Collaborative Strategic Planning Meeting and Western Thalassemia Collaborative. UCSF Benioff Children's Hospital Oakland, Nov 2, 2015.
  • Weyhmiller M. Monitoring Iron Overload Fellows Lecture; Sept 23, 2015; UCSF Benioff Children's Hospital Oakland.
  • Weyhmiller M. Introduction to the SQUID and iron overload program. Guest Lecturer; June 2015; UC Berkeley Biodesign Immersion Experience.

2014

  • Agrawal A. Presentation. Hematology/Oncology Fellows Conference; Children's Hospital Oakland, CA.
  • Agrawal A. Presentation. Pediatric Resident Noon Conference; Children's Hospital Oakland, CA.
  • Rai P. Role of C-Reactive Protein: an inflammatory biomarker in sickle cell disease. Herman and Walter Samuelson Children's Hospital at Sinai, 14th Annual Harry Gordon, MD Resident Scholarly Activity Day, 2014.
  • Rai P. Autoimmune Cytopenia. October 2014; UCSF Benioff Children's Hospital Oakland, Oral faculty presentation educational conference.
  • Rai P. Langerhans cell histiocytosis. March 2014; UCSF Benioff Children's Hospital Oakland, Oral faculty presentation educational conference.
  • Rai P. Leukemia in Down Syndrome. August 2014; UCSF Benioff Children's Hospital Oakland, Oral faculty presentation educational conference.
  • Singer ST. Infertility in transfused thalassemia patients: pathogenesis, diagnosis and clinical approach. Cooley's Anemia Foundation Family Meetings, Chicago, IL; June 2014.
  • Vichinsky E. Alpha Thalassemia Major: New Mutations, Intrauterine Management and Outcomes. Fellows Conference; Nov 17, 2014; UCSF Benioff Children's Hospital Oakland, CA.
  • Weyhmiller M. Introduction to the SQUID and iron overload program. Guest Lecturer; June 2014; UC Berkeley Biodesign Immersion Experience.
  • Walters M. Talk, SCD Symposium. Children's Hospital Oakland Research Institute, CA.
  • Walters M. Talk, UCSF Hematology/Oncology Division, San Francisco, CA.
  • Walters M. Talk, UCSF/CHORI Translational Research Retreat, Oakland, CA.
  • Walters M. Talk, Hematology/Oncology Fellows Conference, Oakland, CA.
  • Walters M. Talk, CHRCO PICU Fellows Conference, Oakland, CA.
  • Walters M. Talk, Children's Hospital Los Angeles, CA.
  • Walters M. Talk, Fred Hutchinson Cancer Research Center, Seattle, WA.
  • Walters M. Talk, Berkeley Stem Cell Center Retreat, Berkeley, CA.
  • Walters M. Talk, AABBUCB Symposium, San Francisco, CA.
  • Walters M. Talk, CIRM Presentation BCL11a, Burlingame, CA.

Profiles:

updated 28 June 2016


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