UCSF Benioff Children's Hospital Oakland
Hematology/Oncology Department
UCSF Benioff Children's Hospital Oakland


Recent Faculty Publications (2014 - 2016)

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Books:

2015:

book: Supportive Care in Pediatric Oncology book: Emerging Therapies Targeting the Pathophysiology of Sickle Cell Disease

2014:


Book Chapters:

2016:

  • Agrawal AK, Shah SS. Pediatrics. In: Gulati A, Puttanniah V, Byas-Smith M, eds. Essentials of Interventional Cancer Pain Management. New York: Springer; 2016 (in press).
  • Agrawal AK, Feusner J. Supportive Care of Patients with Cancer. In: Lanzkowsky P, Lipton JM, Fish JD, eds. Lanzkowsky's Manual of Pediatric Hematology and Oncology. 6th ed: Springer; 2016. http://www.amazon.com/Lanzkowskys-Manual-Pediatric-Hematology-Oncology/dp/0128013680.
  • Rai P, Vichinsky E. COMMENTARY on: "Controlled Trial of Transfusion for Silent Cerebral Infarcts in Sickle Cell Anemia". In: Cabana MD, Goldstein AM, De Gialluly PS, Schroeder A, eds. Year Book of Pediatrics 2016. Philadelphia, PA: Elsevier Mosby; 2016. http://store.elsevier.com/product.jsp?isbn=00843954.
  • Walters MC. Hematopoietic cell transplantation for sickle cell disease. In: Forman SJ, Negris RS, Antin J, Applebaum FR, eds. Hematopoietic Cell Transplantation. Fifth ed. (March 2016). Malden, MA: Blackwell Science; 2016. http://www.wiley.com/WileyCDA/WileyTitle/productCd-1118416120.html.
  • Winstead M, Vichinsky E. Sickle Cell Disease: Management of Complications. In: Non-Malignant Hematology: Expert Clinical Perspective. Springer; 2016 (in press).

2015:

2014:


Journal Articles:

2015:

  • Ballas SK, Vichinsky EP. Is the medical home for adult patients with sickle cell disease a reality or an illusion? Hemoglobin 2015;39 2:130-3. http://www.ncbi.nlm.nih.gov/pubmed/25806421.
  • Burton BK, Berger KI, Lewis GD, Tarnopolsky M, Treadwell M, Mitchell JJ, Muschol N, Jones SA, Sutton VR, Pastores GM, Lau H, Sparkes R, Genter F, Shaywitz AJ, Harmatz P. Safety and physiological effects of two different doses of elosulfase alfa in patients with morquio a syndrome: A randomized, double-blind, pilot study. Am J Med Genet A 2015;167A 10:2272-81. http://www.ncbi.nlm.nih.gov/pubmed/26069231.
  • Day LL, Murray E, Treadwell MJ, Lubin BH. Teaching About Genetics and Sickle Cell Disease in Fifth Grade. Journal of the National Medical Association 2015;Feb 107 (1):4-10. http://www.chori.org/Education/SEPA/Teaching%20Genetics%20and%20SCD_to%20fith%20graders.pdf.
  • Dix D, Aplenc R, Bowes L, Cellot S, Ethier MC, Feusner J, Gillmeister B, Johnston DL, Lewis V, Michon B, Mitchell D, Portwine C, Price V, Silva M, Stobart K, Yanofsky R, Zelcer S, Beyene J, Sung L. Impact of registration on clinical trials on infection risk in pediatric acute myeloid leukemia. Int J Cancer 2015. http://www.ncbi.nlm.nih.gov/pubmed/26515793.
  • Dowling MM, Ramaciotti C, Kanter J, Osunkwo I, Inusa B, Lyer R, Kwiatkovvski J, Johnson C, Rhodes MM, Owen W, Strouse JJ, Quinn C, Panepinto JA, Neumayr L, Sarnaik S, Hynan LS, Plumb P, Kirkham F. Increased Prevalence of Potential Right-to-Left Shunting in Children with Sickle Cell Anemia and Stroke. Stroke 2015;46. <Go to ISI>://WOS:000349634701315
  • Fung EB, Gildengorin G, Talwar S, Hagar L, Lal A. Zinc status affects glucose homeostasis and insulin secretion in patients with thalassemia. Nutrients 2015;7 6:4296-307. http://www.ncbi.nlm.nih.gov/pubmed/26043030.
  • Gardner K, Hoppe C, Mijovic A, Thein SL. How we treat delayed haemolytic transfusion reactions in patients with sickle cell disease. Br J Haematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25967919.
  • Hagar RW. Teasing Apart Pain in Sickle Cell Disease. Eur J Haematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25645541.
  • Harmatz P, Treadwell M, Burton BK, Mitchell J, Muschol N, Jones S, Pastores G, Lau H, Sparkes R, Sutton VR, Genter F, Haller C, Shaywitz A. Impact of elosulfase alfa on pain in patients with Morquio syndrome type A. Molecular Genetics and Metabolism 2015;114 2:S51-S2. http://www.sciencedirect.com/science/article/pii/S1096719214004843.
  • Heeney MM, Hoppe CC, Abboud MR, Inusa B, Kanter J, Ogutu B, Brown PB, Heath LE, Jakubowski JA, Zhou C, Zamoryakhin D, Agbenyega T, Colombatti R, Hassab HM, Nduba VN, Oyieko JN, Robitaille N, Segbefia CI, Rees DC, Investigators D. A Multinational Trial of Prasugrel for Sickle Cell Vaso-Occlusive Events. N Engl J Med 2015. http://www.ncbi.nlm.nih.gov/pubmed/26644172.
  • Hoppe CC, Styles L, Heath LE, Zhou C, Jakubowski JA, Winters KJ, Brown PB, Rees DC, Heeney MM. Design of the DOVE (Determining Effects of Platelet Inhibition on Vaso-Occlusive Events) Trial: A Global Phase 3 Double-Blind, Randomized, Placebo-Controlled, Multicenter Study of the Efficacy and Safety of Prasugrel in Pediatric Patients With Sickle Cell Anemia Utilizing a Dose Titration Strategy. Pediatr Blood Cancer 2015. http://www.ncbi.nlm.nih.gov/pubmed/26402148.
  • Kanter J, Telen MJ, Hoppe C, Roberts CL, Kim JS, Yang X. Validation of a novel point of care testing device for sickle cell disease. BMC Med 2015;13:225. http://www.ncbi.nlm.nih.gov/pubmed/26377572.
  • Kelly S, Deng X, Hoppe C, Styles L. A pilot randomized trial of red blood cell transfusion for acute treatment of vaso-occlusive pain episodes in sickle cell anaemia. Br J Haematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25833727.
  • Khurana M, Lee B, Feusner JH. Fever at Diagnosis of Pediatric Acute Lymphoblastic Leukemia: Are Antibiotics Really Necessary? J Pediatr Hematol Oncol 2015;37 7:498 -501. http://www.ncbi.nlm.nih.gov/pubmed/26376233.
  • Khurana M, Fung EB, Vichinsky E, Theil EC. Dietary ferritin iron, equally bioavailable to non-heme ferrous iron, may be safely consumed in thalassemia intermedia with risk for iron overload. Am J Clin Nutr 2015 (submitted).
  • Lal A, Patterson L, Goldrich A, Marsh A. Point-of-care end-tidal carbon monoxide reflects severity of hemolysis in sickle cell anemia. Pediatr Blood Cancer 2015;62 5:912-4. http://www.ncbi.nlm.nih.gov/pubmed/25683629.
  • Lee DW, Doh I, Kuypers FA, Cho YH. Sub-population analysis of deformability distribution in heterogeneous red blood cell population. Biomed Microdevices 2015;17 6:102. http://www.ncbi.nlm.nih.gov/pubmed/26383009.
  • Marsh A, Schiffelers R, Kuypers F, Larkin S, Gildengorin G, van Solinge W, Hoppe C. Microparticles as biomarkers of osteonecrosis of the hip in sickle cell disease. Br J Haematol 2015;168 1:135-8. http://www.ncbi.nlm.nih.gov/pubmed/25196812.
  • McCann JC, Shigenaga MK, Mietus-Snyder ML, Lal A, Suh JH, Krauss RM, Gildengorin GL, Goldrich AM, Block DS, Shenvi SV, McHugh TH, Olson DA, Ames BN. A multicomponent nutrient bar promotes weight loss and improves dyslipidemia and insulin resistance in the overweight/obese: chronic inflammation blunts these improvements. FASEB J 2015;29 8:3287-301. http://www.ncbi.nlm.nih.gov/pubmed/25900806.
  • Meloni A, Detterich J, Pepe A, Harmatz P, Coates TD, Wood JC. Pulmonary hypertension in well-transfused thalassemia major patients. Blood Cells Mol Dis 2015;54 2:189-94. http://www.ncbi.nlm.nih.gov/pubmed/25488617.
  • Morris CR, Kim HY, Klings ES, Wood J, Porter JB, Trachtenberg F, Sweeters N, Olivieri NF, Kwiatkowski JL, Virzi L, Hassell K, Taher A, Neufeld EJ, Thompson AA, Larkin S, Suh JH, Vichinsky EP, Kuypers FA, Thalassemia Clinical Research N. Dysregulated arginine metabolism and cardiopulmonary dysfunction in patients with thalassaemia. Br J Haematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25907665.
  • Qayed M, Khurana M, Hilinski J, Gillespie S, McCracken C, Applegate K, Chiang K-Y, Horan J. Risk for CMV reactivation in children undergoing allogeneic hematopoietic stem cell transplantation. Pediatric Blood & Cancer 2015;62 2:364-6. http://onlinelibrary.wiley.com/doi/10.1002/pbc.25237/abstract.
  • Singer ST, Killilea D, Suh JH, Wang ZJ, Yuan Q, Ivani K, Evans P, Vichinsky E, Fischer R, Smith JF. Fertility in transfusion-dependent thalassemia men: effects of iron burden on the reproductive axis. Am J Hematol 2015;90 9:E190-2. http://www.ncbi.nlm.nih.gov/pubmed/26044409.
  • Soupene E, Kuypers FA. Ligand binding to the ACBD6 protein regulates the acyl-CoA transferase reactions in membranes. J Lipid Res 2015;56 10:1961-71. http://www.ncbi.nlm.nih.gov/pubmed/26290611.
  • Soupene E, Wang D, Kuypers FA. Remodeling of host phosphatidylcholine by Chlamydia acyltransferase is regulated by acyl-CoA binding protein ACBD6 associated with lipid droplets. Microbiologyopen 2015. http://www.ncbi.nlm.nih.gov/pubmed/25604091.
  • Tang H, Ho H, Wu P, Chen S, Kuypers FA, Cheng M, Chiu DT. Inability to Maintain GSH Pool in G6PD-Deficient Red Cells Causes Futile AMPK Activation and Irreversible Metabolic Disturbance. Antioxid Redox Signal 2015. http://www.ncbi.nlm.nih.gov/pubmed/25556665.
  • Treadwell M, Johnson S, Sisler I, Bitsko M, Gildengorin G, Medina R, Barreda F, Major K, Telfair J, Smith WR. Development of a sickle cell disease readiness for transition assessment. Int J Adolesc Med Health 2015. http://www.ncbi.nlm.nih.gov/pubmed/26226115.
  • Treadwell M, Johnson S, Sisler I, Bitsko M, Gildengorin G, Medina R, Barreda F, Major K, Telfair J, Smith WR. Self-efficacy and readiness for transition from pediatric to adult care in sickle cell disease. Int J Adolesc Med Health 2015. http://www.ncbi.nlm.nih.gov/pubmed/26226116.
  • Treadwell MJ, Anie KA, Grant AM, Ofori-Acquah SF, Ohene-Frempong K. Using Formative Research to Develop a Counselor Training Program for Newborn Screening in Ghana. J Genet Couns 2015;24 2:267-77. http://www.ncbi.nlm.nih.gov/pubmed/25193810.
  • Treadwell MJ, Barreda F, Kaur K, Gildengorin G. Emotional distress, barriers to care and health-related quality of life in sickle cell disease. J Clin Outcomes Manage 2015;22 1:10-20. http://www.turner-white.com/pdf/jcom_jan15_sickle.pdf.
  • Trobaugh-Lotrario AD, Meyers RL, Feusner JH. Outcomes of Patients With Relapsed Hepatoblastoma Enrolled on Children's Oncology Group (COG) Phase I and II Studies. J Pediatr Hematol Oncol 2015. http://www.ncbi.nlm.nih.gov/pubmed/26583620.
  • Tubman VN, Fung EB, Vogiatzi M, Thompson AA, Rogers ZR, Neufeld EJ, Kwiatkowski JL, Thalassemia Clinical Research N. Guidelines for the Standard Monitoring of Patients With Thalassemia: Report of the Thalassemia Longitudinal Cohort. J Pediatr Hematol Oncol 2015;37 3:e162-9. http://www.ncbi.nlm.nih.gov/pubmed/26201037.
  • Vichinsky E. Non-transfusion-dependent thalassemia and thalassemia intermedia: epidemiology, complications, and management. Curr Med Res Opin 2015:1-14. http://www.ncbi.nlm.nih.gov/pubmed/26479125.
  • Walters MC. Update of hematopoietic cell transplantation for sickle cell disease. Curr Opin Hematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25767957.
  • Walters MC, De Castro LM, Sullivan KM, Krishnamurti L, Kamani N, Bredeson C, Neuberg D, Hassell KL, Farnia S, Campbell A, Petersdorf E. Indications and Results of HLA-Identical Sibling Hematopoietic Cell Transplantation for Sickle Cell Disease. Biol Blood Marrow Transplant 2015. http://www.ncbi.nlm.nih.gov/pubmed/26500093.
  • Walters MC, MacKenzie TC. A booster shot to cure hemoglobinopathies. Blood 2015;126 10:1159-61. http://www.ncbi.nlm.nih.gov/pubmed/26337353.
  • Wonkam A, Makani J, Ofori-Aquah S, Nnodu OE, Treadwell M, Royal C, Ohene-Frempong K, as members of the HAC. Sickle cell disease and H3Africa: enhancing genomic research on cardiovascular diseases in African patients. Cardiovasc J Afr 2015;26 2 Suppl 1:S50-5. http://www.ncbi.nlm.nih.gov/pubmed/25962948.
  • Zerofsky M, Ryder M, Bhatia S, Stephensen CB, King J, Fung EB. Effects of early vitamin D deficiency rickets on bone and dental health, growth and immunity. Matern Child Nutr 2015. http://www.ncbi.nlm.nih.gov/pubmed/25850574.

2014:

  • Afshar M, Birnbaum D, Golden C. Review of dextromethorphan administration in 18 patients with subacute methotrexate central nervous system toxicity. Pediatr Neurol 2014;50 6:625-9. http://www.ncbi.nlm.nih.gov/pubmed/24742799.
  • Afzal SY, Wender AR, Jones MD, Fung EB, Pico EL. The effect of low magnitude mechanical stimulation (LMMS) on bone density in patients with Rett syndrome: a pilot and feasibility study. J Pediatr Rehabil Med 2014;7 2:167-78. http://www.ncbi.nlm.nih.gov/pubmed/25096869.
  • Anglemyer A, Agrawal AK, Rutherford GW. Treatment of Kaposi sarcoma in children with HIV-1 infection. Cochrane Database Syst Rev 2014;1:CD009826. http://www.ncbi.nlm.nih.gov/pubmed/24464843.
  • Cui J, Azimi M, Hoppe CC. Detection of a novel betadelta-globin fusion gene, anti-lepore Hb CHORI (beta(through IVS-I-57)/delta(from IVS-I-101)), by multiplex ligation-dependent probe amplification. Hemoglobin 2014;38 1:60-3. http://www.ncbi.nlm.nih.gov/pubmed/24102354.
  • Dagri JN, Evans A, Torkildson JC, Portnow J, Ashby LS, Zakotnik B, Brown RJ, Dhall G, Finlay JL. Feasibility of an Attenuated Maintenance chemotherapy Regimen Directed at Adolescents and Young Adults with Newly Diagnosed Localized Medulloblastoma and Other Central Nervous System Embryonal Tumors. J Adolescent and Young Adult Oncology 2014;3 3:106-11.
  • Dang DN, Morris HD, Feusner JH, Koduru P, Wilson K, Timmons CF, Cavalier M, Luu HS. Therapy-induced Secondary Acute Myeloid Leukemia With t(11;19)(q23;p13.1) in a Pediatric Patient With Relapsed Acute Promyelocytic Leukemia. J Pediatr Hematol Oncol 2014;36 8:e546-8. http://www.ncbi.nlm.nih.gov/pubmed/24942021.
  • Delgado EM, Cho CS, Gildengorin G, Leibovich SA, Morris CR. Parental Asthma Education and Risks for Nonadherence to Pediatric Asthma Treatments. Pediatr Emerg Care 2014;30 11:782-7 10.1097/PEC.0000000000000259. http://journals.lww.com/pec-online/Fulltext/2014/11000/Parental_Asthma_Education_and_Risks_for.3.aspx
  • Derderian SC, Jeanty C, Walters MC, Vichinsky E, MacKenzie TC. In utero hematopoietic cell transplantation for hemoglobinopathies. Front Pharmacol 2014;5:278. http://www.ncbi.nlm.nih.gov/pubmed/25628564.
  • Gladwin MT, Barst RJ, Gibbs JS, Hildesheim M, Sachdev V, Nouraie M, Hassell KL, Little JA, Schraufnagel DE, Krishnamurti L, Novelli E, Girgis RE, Morris CR, Berman Rosenzweig E, Badesch DB, Lanzkron S, Castro OL, Taylor JGt, Goldsmith JC, Kato GJ, Gordeuk VR, Machado RF, Walk Phaast investigators. Risk factors for death in 632 patients with sickle cell disease in the United States and United Kingdom. PloS one. 2014;9(7):e99489. Epub 2014/07/06. doi: 10.1371/journal.pone.0099489. PubMed PMID: 24988120; PubMed Central PMCID: PMC4079316. http://journals.plos.org/plosone/article?id=10.1371/journal.pone.0099489.
  • Green ST, Martin MB, Haines D, Carson S, Coates T, Oliveros O, Gerstenberger E, Trachtenberg F, Kwiatkowski JL, Thalassaemia Clinical Research N. Variance of pain prevalence and associated severity during the transfusion cycle of adult thalassaemia patients. Br J Haematol 2014;166 5:797-800. http://www.ncbi.nlm.nih.gov/pubmed/24805301.
  • Hastings C, Gaynon PS, Nachman JB, Sather HN, Lu X, Devidas M, Seibel NL. Increased post-induction intensification improves outcome in children and adolescents with a markedly elevated white blood cell count (>/=200 x 10 /l) with T cell acute lymphoblastic leukaemia but not B cell disease: a report from the Children's Oncology Group. Br J Haematol 2014. http://www.ncbi.nlm.nih.gov/pubmed/25308804.
  • Hoppe CC. Inflammatory mediators of endothelial injury in sickle cell disease. Hematol Oncol Clin North Am 2014;28 2:265-86. http://www.ncbi.nlm.nih.gov/pubmed/24589266.
  • Karafin MS, Graminske S, Erickson P, Walters MC, Scott EP, Carter S, Padmanabhan A. Evaluation of the Spectra Optia apheresis system for mononuclear cell (MNC) collection in G-CSF mobilized and nonmobilized healthy donors: results of a multicenter study. J Clin Apher 2014;29 5:273-80. http://www.ncbi.nlm.nih.gov/pubmed/24677347.
  • Karski EE, Dvorak CC, Leung W, Miller W, Shaw PJ, Qayed M, Katsanis E, Feusner JH. Treatment of Hepatoblastoma With High-dose Chemotherapy and Stem Cell Rescue: The Pediatric Blood and Marrow Transplant Consortium Experience and Review of the Literature. J Pediatr Hematol Oncol 2014. http://www.ncbi.nlm.nih.gov/pubmed/24577552.
  • Keller SD, Yang M, Treadwell MJ, Werner EM, Hassell KL. Patient reports of health outcome for adults living with sickle cell disease: development and testing of the ASCQ-Me item banks. Health Qual Life Outcomes 2014;12:125. http://www.ncbi.nlm.nih.gov/pubmed/25146160.
  • Klaassen RJ, Barrowman N, Merelles-Pulcini M, Vichinsky E, Sweeters N, Kirby-Allen M, Neufeld EJ, Kwiatkowski JL, Wu J, Vickars L, Blanchette VS, Forgie M, Yamashita R, Wong-Rieger D, Young NL. Validation and reliability of a disease-specific quality of life measure (the TranQol) in adults and children with thalassaemia major. Br J Haematol 2014;164 3:431-7. http://www.ncbi.nlm.nih.gov/pubmed/24180641.
  • Kutny MA, Gregory J, Jr., Feusner JH. Treatment of paediatric APL: how does the therapeutic approach differ from adults? Best Pract Res Clin Haematol 2014;27 1:69-78. http://www.ncbi.nlm.nih.gov/pubmed/24907019.
  • Kuypers FA. Hemoglobin S Polymerization and Red Cell Membrane Changes. Hematol Oncol Clin North Am 2014;28 2:155-79. http://www.ncbi.nlm.nih.gov/pubmed/24589260.
  • Mackin RS, Insel P, Truran D, Vichinsky E, Neumayr LD, Armstrong FD, Gold JI, Kesler K, Brewer J, Weiner MW, Neuropsychological D, Neuroimaging Adult Sickle Cell Anemia Study G. Neuroimaging abnormalities in adults with sickle cell anemia: associations with cognition. Neurology 2014;82 10:835-41. http://www.ncbi.nlm.nih.gov/pubmed/24523480.
  • Marsh A, Golden C, Hoppe C, Quirolo K, Vichinsky E. Renal medullary carcinoma in an adolescent with sickle cell anemia. Pediatr Blood Cancer 2014;61 3:567. http://www.ncbi.nlm.nih.gov/pubmed/24108577.
  • Paulukonis ST, Harris WT, Coates TD, Neumayr L, Treadwell M, Vichinsky E, Feuchtbaum LB. Population based surveillance in sickle cell disease: Methods, findings and implications from the California registry and surveillance system in hemoglobinopathies project (RuSH). Pediatr Blood Cancer 2014;61 12:2271-6. http://www.ncbi.nlm.nih.gov/pubmed/25176145.
  • Polgreen LE, Thomas W, Fung E, Viskochil D, Stevenson DA, Steinberger J, Orchard P, Whitley CB, Ensrud KE. Low Bone Mineral Content and Challenges in Interpretation of Dual-Energy X-Ray Absorptiometry in Children With Mucopolysaccharidosis Types I, II, and VI. J Clin Densitom 2014;17 1:200-6. http://www.ncbi.nlm.nih.gov/pubmed/23562131.
  • Porter JB, Walter PB, Neumayr LD, Evans P, Bansal S, Garbowski M, Weyhmiller MG, Harmatz PR, Wood JC, Miller JL, Byrnes C, Weiss G, Seifert M, Grosse R, Grabowski D, Schmidt A, Fischer R, Nielsen P, Niemeyer C, Vichinsky E. Mechanisms of plasma non-transferrin bound iron generation: insights from comparing transfused diamond blackfan anaemia with sickle cell and thalassaemia patients. Br J Haematol 2014;167 5:692-6. http://www.ncbi.nlm.nih.gov/pubmed/25209728.
  • Quirolo K, Bertolone S, Hassell K, Howard T, King KE, Rhodes DK, Bill J. The evaluation of a new apheresis device for automated red blood cell exchange procedures in patients with sickle cell disease. Transfusion 2014. http://www.ncbi.nlm.nih.gov/pubmed/25330984.
  • Reid ME, Halter Hipsky C, Hue-Roye K, Hoppe C. Genomic analyses of RH alleles to improve transfusion therapy in patients with sickle cell disease. Blood Cells Mol Dis 2014;52 4:195-202. http://www.ncbi.nlm.nih.gov/pubmed/24309423.
  • Singer ST, Kuypers F, Fineman J, Gildengorin G, Larkin S, Sweeters N, Rosenfeld H, Kurio G, Higa A, Jeng M, Huang J, Vichinsky E. Elevated tricuspid regurgitant jet velocity in subgroups of thalassemia patients: insight into pathophysiology and the effect of splenectomy. Ann Hematol 2014;93 7:1139-48. http://www.ncbi.nlm.nih.gov/pubmed/24577514.
  • Soni S, Boulad F, Cowan MJ, Scaradavou A, Dahake J, Edwards S, Walters MC. Combined umbilical cord blood and bone marrow from HLA-identical sibling donors for hematopoietic stem cell transplantation in children with hemoglobinopathies. Pediatr Blood Cancer 2014;61 9:1690-4. http://www.ncbi.nlm.nih.gov/pubmed/24803091.
  • Stevenson DA, Rudser K, Kunin-Batson A, Fung EB, Viskochil D, Shapiro E, Orchard PJ, Whitley CB, Polgreen LE. Biomarkers of bone remodeling in children with mucopolysaccharidosis types I, II, and VI. J Pediatr Rehabil Med 2014;7 2:159-65. http://www.ncbi.nlm.nih.gov/pubmed/25096868.
  • Suh J, Kanathezhath B, Shenvi S, Guo H, Zhou A, Tiwana A, Kuypers F, Ames B, Walters M. Thiol/Redox Metabolomic Profiling Implicates GSH Dysregulation in Early Experimental Graft versus Host Disease (GVHD). PLoS ONE 2014;9 (2):e88868. http://www.plosone.org/article/info%3Adoi%2F10.1371%2Fjournal.pone.0088868.
  • Te Vruchte D, Speak AO, Wallom KL, Al Eisa N, Smith DA, Hendriksz CJ, Simmons L, Lachmann RH, Cousins A, Hartung R, Mengel E, Runz H, Beck M, Amraoui Y, Imrie J, Jacklin E, Riddick K, Yanjanin NM, Wassif CA, Rolfs A, Rimmele F, Wright N, Taylor C, Ramaswami U, Cox TM, Hastings C, Jiang X, Sidhu R, Ory DS, Arias B, Jeyakumar M, Sillence DJ, Wraith JE, Porter FD, Cortina-Borja M, Platt FM. Relative acidic compartment volume as a lysosomal storage disorder-associated biomarker. J Clin Invest 2014. http://www.ncbi.nlm.nih.gov/pubmed/24487591.
  • Theil EC. IRE mRNA riboregulators use metabolic iron (Fe) to control mRNA activity and iron chemistry in animals. Metallomics 2014. http://www.ncbi.nlm.nih.gov/pubmed/25209685.
  • Trachtenberg FL, Gerstenberger E, Xu Y, Mednick L, Sobota A, Ware H, Thompson AA, Neufeld EJ, Yamashita R, Thalassemia Clinical Research N. Relationship among chelator adherence, change in chelators, and quality of life in thalassemia. Qual Life Res 2014;23 8:2277-88. http://www.ncbi.nlm.nih.gov/pubmed/24682717.
  • Treadwell MJ, Anie KA, Grant AM, Ofori-Acquah SF, Ohene-Frempong K. Using Formative Research to Develop a Counselor Training Program for Newborn Screening in Ghana. J Genet Couns 2014. http://www.ncbi.nlm.nih.gov/pubmed/25193810.
  • Treadwell MJ, Bell M, Leibovich SA, Barreda F, Marsh A, Gildengorin G, Morris CR. A Quality Improvement Initiative to Improve Emergency Department Care for Pediatric Patients with Sickle Cell Disease. J Clin Outcomes Manage 2014;21 2:62-70. http://www.hospitalphysician.com/pdf/jcom_feb14_pediatric.pdf.
  • Treadwell MJ, Hassell K, Levine R, Keller S. Adult Sickle Cell Quality of Life Measurement Information System (ASCQ-Me): Conceptual Model Based on Review of the Literature and Formative Research. Clin J Pain 2014. http://www.ncbi.nlm.nih.gov/pubmed/24300219.
  • Trobaugh-Lotrario AD, Venkatramani R, Feusner JH. Hepatoblastoma in Children With Beckwith-Wiedemann Syndrome: Does it Warrant Different Treatment? J Pediatr Hematol Oncol 2014. http://www.ncbi.nlm.nih.gov/pubmed/24608075.
  • Ubogy S, Olson K. The Trauma Symptom Checklist for Children and Misdiagnosis of PTSD in A Youth with Acute Lymphocytic Leukemia: A Brief Report. Journal of Child & Adolescent Trauma 2014:1-3. http://rd.springer.com/article/10.1007/s40653-014-0004-1
  • Vichinsky E, Neumayr L, Trimble S, Giardina PJ, Cohen AR, Coates T, Boudreaux J, Neufeld EJ, Kenney K, Grant A, Thompson AA, Investigators CDCT. Transfusion complications in thalassemia patients: a report from the Centers for Disease Control and Prevention (CME). Transfusion 2014;54 4:972-81; quiz 1. http://www.ncbi.nlm.nih.gov/pubmed/23889533.
  • Wagner JE, Jr., Eapen M, Carter S, Wang Y, Schultz KR, Wall DA, Bunin N, Delaney C, Haut P, Margolis D, Peres E, Verneris MR, Walters M, Horowitz MM, Kurtzberg J, Blood, Marrow Transplant Clinical Trials N. One-unit versus two-unit cord-blood transplantation for hematologic cancers. N Engl J Med 2014;371 18:1685-94. http://www.ncbi.nlm.nih.gov/pubmed/25354103.
  • Walters MC. Update of hematopoietic cell transplantation for sickle cell disease. Curr Opin Hematol 2015. http://www.ncbi.nlm.nih.gov/pubmed/25767957.
  • Wun T, Styles L, DeCastro L, Telen MJ, Kuypers F, Cheung A, Kramer W, Flanner H, Rhee S, Magnani JL, Thackray H. Phase 1 study of the E-selectin inhibitor GMI 1070 in patients with sickle cell anemia. PLoS One 2014;9 7:e101301. http://www.ncbi.nlm.nih.gov/pubmed/24988449.
  • Zaky W, Dhall G, Ji L, Haley K, Allen J, Atlas M, Bertolone S, Cornelius A, Gardner S, Patel R, Pradhan K, Shen V, Thompson S, Torkildson J, Sposto R, Finlay JL. Intensive induction chemotherapy followed by myeloablative chemotherapy with autologous hematopoietic progenitor cell rescue for young children newly-diagnosed with central nervous system atypical teratoid/rhabdoid tumors: the Head Start III experience. Pediatr Blood Cancer 2014;61 1:95-101. http://www.ncbi.nlm.nih.gov/pubmed/23934933.
  • Zhang L, Samad A, Pombo-de-Oliveria MS, Seelo G, Smith MT, Feusner J, Wiemels JL, Buffler PA, Metayer C. Global characteristics of childhood acute promyelocytic leukemia. Blood Reviews 2014;Sep 30 2014. http://www.sciencedirect.com/science/article/pii/S0268960X14000824.

Editorials:

2015:

2014:


Letters:

2014:

  • Klings ES, Machado RF, Morris CR, Gordeuk VR, Kato GJ, Ataga KI, Castro O, Hsu L, Telen MJ, Krishnamurti L, Steinberg MH, Gladwin MT, Diagnosis ATSCGft, Treatment of Pulmonary Hypertension in Sickle Cell Disease C. Reply: Practice guideline for pulmonary hypertension in sickle cell: direct evidence needed before universal adoption. Am J Respir Crit Care Med. 2014;190(2):238-40. Epub 2014/07/16. doi: 10.1164/rccm.201404-0733LE. PubMed PMID: 25025360; PubMed Central PMCID: PMC4226058. a href="http://www.atsjournals.org/doi/abs/10.1164/rccm.201404-0733LE#.VLXc-yvF_Tc.
  • Klings ES, Vichinsky E, Morris CR. Response to "Efficacy and safety of sildenafil for the treatment of severe pulmonary hypertension in patients with hemoglobinopathies: results from a long-term follow up " Haematologica 2014;99(2):e17-18. Haematologica 2014;99 2:e19. http://www.ncbi.nlm.nih.gov/pubmed/24497564.
  • Klings ES, Morris CR, Hsu LL, Castro O, Gladwin MT, Mubarak KK. Pulmonary hypertension of sickle cell disease beyond classification constraints. J Am Coll Cardiol 2014;63 25 Pt A:2881-2. http://www.ncbi.nlm.nih.gov/pubmed/24794120.
  • Reddy-Holdcraft S, Mehta PS, Agrawal AK. Paclitaxel for relapsed or recurrent HIV-associated pediatric Kaposi's sarcoma. AIDS 2014;28 5:800-2. http://www.ncbi.nlm.nih.gov/pubmed/24983546.
  • Slone JS, Agrawal AK, Mehta PS, Mazhani L, Motumise K, Anabwani G, Poplack DG. Reply to "Childhood Cancer in Africa". Pediatr Blood Cancer 2014;61 8:1524. http://www.ncbi.nlm.nih.gov/pubmed/24519963.

Abstracts:

2016:

  • Trobaugh-Lotrario AD, Feusner J. Clinical Characteristics of Patients with Familial Adenomatous Polyposis (FAP) and Hepatoblastoma (HB) International Pediatric Liver Tumor Symposium. Houston, Texas; Feb 25-26, 2016. Texas Children's Hospital.

2015:

  • Cappelli B, Bernaudin F, Ruggeri A, Labopin M, Volt F, Simoes BP, Ferster A, Dupont S, de la Fuente J, Dalle J-H, Zecca M, Robin M, Walters MC, Dhedin N, Michel G, Lutz P, Neven B, Bertrand Y, Vannier JP, Ayas M, Matthes S, Elayoubi H, Devergie A, Kenzey C, Locatelli F, Peters C, Rocha V, Eapen M, Gluckman E. Hematopoietic Stem Cell Transplantation from HLA Identical Sibling Forsickle Cell Disease an International Survey on Behalf of Eurocord-Monacord, EBMT Paediatric Disease Working Party and CIBMTR. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL; Dec 5-8, 2015. Blood 126(23); 541. http://www.bloodjournal.org/content/126/23/541.abstract..
  • Cavazzana M, Ribeil J-A, Payen E, Suarez F, Beuzard Y, Touzot F, Cavallesco R, Lefrere F, Chretien S, Bourget P, Monpoux F, Pondarre C, Neven B, Schmidt M, von Kalle C, Kuypers FA, Sandler L, Soni S, Hermine O, Blanche S, De Montalembert M, Hacien-Bey-Abina S, Leboulch P. Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta AT87Q-Globin Vector. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 202. http://www.bloodjournal.org/content/126/23/202.abstract..
  • Field JJ, Majerus EM, Ataga KI, Vichinsky EP, Eaton C, Mazanet R, Nathan DG. NKTT120 Safely Depletes iNKT Cells in Stable Adult Sickle Cell Patients in a Phase 1 Trial. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 2178. http://www.bloodjournal.org/content/126/23/2178.abstract..
  • Gilbert S, Scott E, Thomas L, Boudreau J, Carrion V, Kwiatkowski J, Beatty J, Batts A, Thompson A, Welty S, Vichinsky E, Saykin AJ, Russell E, Eile J, Neufeld E, Carson S, Coates T, Sayers C, Butler C, Cioffi G. Patient outreach methods used to locate patients with thalassemia in the United States. 10th Annual Cooley's Anemia Symposium, October 18-22, 2015. Chicago, IL.
  • Heeney M, George A, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E. Clinical outcomes in pediatric and adult patients with sickle cell disease: Results of a 3-year, prospective, longitudinal noninterventional registry study. SCDAA 43rd Annual Convention; Sept 23-26, 2015. Baltimore, MD.
  • Hoppe C. Controversies in Managing Sickle Cell Disease: NCAA vs AAP vs NIH Recommendations. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.305-312. University of California, San Francisco, School of Medicine.
  • Hoppe CC, Jacob E, Kuypers FA, Styles L. Simvastatin Reduces Frequency of Vaso-Occlusive Pain in Sickle Cell Disease: A Pilot Efficacy Trial. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 545. http://www.bloodjournal.org/content/126/23/545.abstract.
  • Kanter J, Walters MC, Hsieh M, Thompson AA, Krishnamurti L, Kwiatkowski J, Kamble RT, von Kalle C, Kuypers FA, Cavazzana M, Leboulch P, Sandler L, Soni S, Tisdale JF. Initial Results from Study Hgb-206: A Phase 1 Study Evaluating Gene Therapy By Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo with the Lentiglobin BB305 Lentiviral Vector in Subjects with Severe Sickle Cell Disease. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 3233. http://www.bloodjournal.org/content/126/23/3233.abstract.
  • Krishnamurti L, Sullivan KM, Kamani NR, Waller EK, Abraham A, Campigotto F, Zhang W, Smith S, Hassell KL, Decastro L, Wu CJ, Neuberg DS, Walters MC. Results of a Multicenter Pilot Investigation of Bone Marrow Transplantation in Adults with Sickle Cell Disease (STRIDE). 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 543. http://www.bloodjournal.org/content/126/23/543.abstract.
  • Kutny MA, Alonzo TA, Gerbing RB, Wang Y-C, Fu C, Meshinchi S, Gamis AS, Feusner JH, Gregory J. Results of a Phase III Trial Including Arsenic Trioxide Consolidation for Pediatric Patients with Acute Promyelocytic Leukemia (APL): A Report from the Children's Oncology Group Study AAML0631. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL; Dec 5-8, 2015. Blood 126(23); 219. http://www.bloodjournal.org/content/126/23/219.abstract.
  • Lal A. Alpha Thalassemia Hb H Disease: An Emerging Public Health Problem. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.297-303. University of California, San Francisco, School of Medicine.
  • Lalefar NR, Hagar W. A Comparison of Hematologic Parameters in Patients with Sickle Cell Disease Undergoing Red Cell Exchange Using Terumo BCT Spectra Optia and COBE Spectra Apheresis Systems. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 4743. http://www.bloodjournal.org/content/126/23/4743.abstract.
  • Lalefar NR, Walters MC. Graft Failure after Hematopoietic Cell Transplantation for Hemoglobin Disorders: Successful Application of a Rescue Regimen. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 5460. http://www.bloodjournal.org/content/126/23/5460.abstract.
  • Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris C. Are we missing the mark? Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest syndrome (ACS). Pediatric Academy Society Annual Meeting. San Diego, CA; April 2015.
  • MacKenzie T, Walters M, Vichinsky E. In utero transplantation in patients with Alpha Thalassemia Major: the birth of a new therapy. Second International Conference on In Utero Transplantation and Fetal Gene Therapy. London, England; October 9-30, 2015.
  • MacKenzie T, Walters M, Vichinsky E. In utero transplantation in patients with Alpha Thalassemia Major: the birth of a new therapy. Tenth Annual Cooley's Anemia Symposium. Chicago, IL; October 18-22, 2015.
  • Puri L, Matsunaga A. Idiopathic hypereosinophilic syndrome with cardiac thrombus in a four year old girl: a case reportand review of the literature. American Society of Pediatric Hematology/Oncology 28th Annual Meeting. Phoeniz, AZ; May 6-9, 2015. Pedatr Blood & Cancer 62(S1); 629.
  • Rai P, Winstead M, Feusner J. Cerebral metastasis of hepatoblastoma: what is the best therapy? American Society of Pediatric Hematology/Oncology 28th Annual Meeting. Phoeniz, AZ; May 6-9, 2015. Pedatr Blood & Cancer 62(S1); 660.
  • Shenoy S, Eapen M, Wu J, Walters MC, Levine JE, Logan B, Gersten ID, Kamani NR. A Multicenter Phase II Trial of Unrelated Donor Reduced Intensity Bone Marrow Transplantation for Children with Severe Sickle Cell Disease (SCURT): Results of the Blood and Marrow Transplant Clinical Trials Network (BMT CTN 0601) Study. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL; Dec 5-8, 2015. Blood 126(23); 619. http://www.bloodjournal.org/content/126/23/619.abstract.
  • Smith WR, McClish DI, Lottenberg R, Chen I, Villela, Sisler I, Johnson S, Trice D, Sop D, Keller S, Treadwell M, Haywood C. Patient reported outcomes in sickle cell disease: current results from PROMIS, ASCQ-ME, & utility in clinical trials. NHLBI Annual Sickle Cell Disease Clinical Trials Meetings; Aug 18-22, 2015. Bethesda, MD.
  • Vichinsky E, Kwiatkowski J, Giardina P, Paley C, Vekeman F, Cheng W, Damron J, McCormick N, Sasane M, Qui Y, Sheng DM, Thompson A. Epidemiologic and clinical characteristics of thalassemia intermedia in the United States. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 3279. http://www.bloodjournal.org/content/126/23/3279.
  • Walter PB, Hohman L, Rokeby A, Lum J, Hagar R, Stewart M, Lavrisha L, Vichinsky E, Morris CR. The Effects of Glutamine Supplementation on Markers of Autophagy and Apoptosis in Peripheral Blood Mononuclear Cells from Patients with Sickle Cell Disease. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 3412. http://www.bloodjournal.org/content/126/23/3412.abstract.
  • Walter PB, Slater N, Harmatz P, Higa A, Ng V, Weyhmiller M, Evans P, Porter JB, Sweeters N, Price J, Killilea D, Neumayr L, Lal A, Vichinsky E. Iron Level and Monocyte Morphology Predict TLR4 Expression and Reactive Oxygen Species Production Which Influences Chronic Inflammation in -Thalassemia. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL; Dec 5-8, 2015. Blood 126(23); 950. http://www.bloodjournal.org/content/126/23/950.abstract.
  • Walters MC, Rasko J, Hongeng S, Kwiatkowski J, Schiller GJ, Kletzel M, Ho PJ, Vichinsky E, von Kalle C, Cavazzana M, Leboulch P, Petrusich A, Soni S, Thompson AA. Update of Results from the Northstar Study (HGB-204): A Phase 1/2 Study of Gene Therapy for Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex-Vivo with a Lentiviral Beta AT87Q-Globin Vector (LentiGlobin BB305. 57th American Society of Hematology Annual Meeting and Exposition. Orlando, FL Dec 5-8, 2015. Blood 126(23); 201. http://www.bloodjournal.org/content/126/23/201.abstract.

2014:

  • Abikoff CM, Talano J-A, Keever-Taylor CA, Walters MC, Shenoy S, Moore T, Parsons SK, Dozor AJ, Friedman D, Chitti R, Shi Q, Grossman BJ, Weinberg RS, Morris E, Brand P, Foley S, Militano O, Ayello J, Semidei-Pomales M, Baxter-Lowe LA, Cairo MS. Familial Haploidentical (FHI) T-Cell Depleted (TCD) with T-Cell Addback Stem Cell Transplantation for Patients with High-Risk Sickle Cell Disease (SCD) (IND 14359). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2582. http://www.bloodjournal.org/content/124/21/2582.
  • Adams-Graves P, Heeney M, Mueller B, Baltz B, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E. Treatment patterns and clinical outcomes among patients with sickle cell disease: 24-month follow-up on a 3-year, prospective, non-interventional registry. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014. Pediatric Blood & Cancer. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
  • Adisa F, Buchanan I, Morris CR. BiPap use in children with sickle cell disease (SCD) and acute chest syndrome (ACS). 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 2014.
  • Akinsola B, Hagbom R, Zmitrovich A, Kavanagh P, Ashkouti A, Fletcher A, Vinson N, Simon HK, Fleming A, Jain S, Adisa O, Dampier C, Morris CR. Adding intranasal fentanyl (INF) to the management of sickle cell disease (SCD) vaso-occlusive pain episodes (VOE) at a pediatric emergency department (ED): a quality improvement study. 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 2014.
  • Akinsola B, Hagbom R, Zmitrovich A, Kavanagh P, Ashkouti A, Fletcher A, Vinson N, Simon HK, Fleming A, Jain S, Adisa O, Dampier C, Morris CR. More rapid delivery of parenteral analgesia by adding intranasal fentanyl to the management of sickle cell disease vaso-occlusive pain episodes at a pediatric emergency department. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).
  • Badawy SM, Pinckney K, Meier ER, Myers K, Black V, Hastings CA, Hilden J, Zweidler-McKay PA, Stork L, Vaiselbuh SR, Johnson TS. First interim analysis of the ASPHO mentoring program. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
  • Fung EB, Killilea DW, Shenvi S, Haines D, Lavrisha L, Flores B, Higa A, Ahmad T, Lal A. Marginal zinc status associated with altered insulin metabolism in patients with thalassemia. 4th International Society for Zinc Biology Meeting. Asilomar, CA; Sep 14-19, 2014. poster presentation, abstract #FF10.
  • Fung EB, Sushrita N, Haines D, Schroepfer C, Lal A. Dietary Intake Insufficient to Support Nutritional Adequacy in Patients with Thalassemia. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 1361. http://www.bloodjournal.org/content/124/21/1361.
  • Hacker NA, King JC, Van Loan MD, Gertz ER, Adams M, Sawyer A, Fung EB. Calcium supplementation during pregnancy improves tibial bone density at one year post-partum in racially diverse women. Experimental Biology, April 2014. San Diego, CA. #14-7168.
  • Heeney MM, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E, George A. Comparison of Clinical Outcomes Between Adult and Pediatric Patients (pts) with Sickle Cell Disease (SCD): 3-Year (y) Follow-up in a Prospective, Longitudinal, Noninterventional Registry Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4890-. http://www.bloodjournal.org/content/124/21/4890.
  • Keller SD, Treadwell MJ, Yang M, Werner EM, Hassell KL. Patient reports of health outcomes in sickle cell disease: psychometric properties of the Adult Sickle Cell Quality of Life Measurement System. 2nd Global Congress on Sickle Cell Disease. Rio de Janiero, Brazil: November 11-14, 2014. http://www.hemorio.rj.gov.br/CongressoGSCDN/programa.pdf.
  • Khurana M, Kanathezhath B, Feusner J. Recurrent/refractory metastatic osteosarcoma responds to TRAIL therapy. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
  • Khurana M, Vichinsky E, Theil EC. Head-to-head comparison of current clinical iron chelators on cellular ferritin regulation in HEPG2 cell culture model. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
  • Kutny MA, Alonzo TA, Gerbing RB, Wang Y-C, Fu C, Meshinchi S, Gamis AS, Feusner JH, Gregory J. Arsenic Trioxide Is a Well Tolerated Consolidation Regimen in Children with Newly Diagnosed Acute Promyelocytic Leukemia; Toxicity Results of the Children's Oncology Group AAML0631 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 985-. http://www.bloodjournal.org/content/124/21/985.
  • Kutny MA, Geyer S, Laumann KM, Gregory J, Willman CL, Stock W, Larson RA, Powell BL, Feusner JH. A Comparison of Outcomes Between Adolescents and Young Adults (AYA) and Children with Acute Promyelocytic Leukemia (APL): North American Intergroup Study CALGB 9710 (Alliance). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2306-. http://www.bloodjournal.org/content/124/21/2306.
  • Kutny MA, Geyer S, Laumann KM, Gregory J, Willman CL, Stock W, Larson RA, Powell BL, Feusner JH. Effect of Young Age on Outcomes in Pediatric Acute Promyelocytic Leukemia (APL): North American Intergroup Study CALGB 9710 (Alliance). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2301-. http://www.bloodjournal.org/content/124/21/2301.
  • Kutny MA, Rajpurkar M, Alonzo TA, Gerbing RB, Gamis AS, Feusner JH, Gregory J. Evaluation of ISTH DIC Score to Predict Significant Bleeding and Thrombosis Events in Pediatric Acute Promyelocytic Leukemia; A Report from the Children's Oncology Group AAML0631 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 3669-. http://www.bloodjournal.org/content/124/21/3669.
  • Lal A, Patterson L, Goldrich A, Marsh A, Yen K, Bhatnagar A. Detection of elevated end-tidal carbon monoxide concentration in children with sickle cell anemia. PAS/ASPR Joint Meeting. Vancouver, Canada: May 3-6, 2014. Pediatric Academic Societies and Asian Society for Pediatric Research.
  • Lal A, Yen K, Patterson L, Goldrich A, Marsh AM, Bhatnagar A. Elevated End-Tidal Carbon Monoxide Concentration in Children with Sickle Cell Anemia. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 1390-. http://www.bloodjournal.org/content/124/21/1390.
  • Lalefar NR, Walters M. Graft failure after hematopoietic cell transplantation for hemoglobionpathies; successful rescue with alternate donors. Annual Sickle Cell Disease Research and Educational Symposium and 37th National Sickle Cell Disease Scientific Meeting. Miami, FL; April 11-14, 2014.
  • Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris CR. Are we missing the mark? Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest syndrome (ACS). 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 2014.
  • Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris CR. Are we missing the mark? Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest syndrome (ACS). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).
  • Lee JH, Rademaker AW, Powell BL, Geyer S, Larson RA, Gregory J, Hijiya N, Feusner JH. Obesity Does Not Affect the Recurrence Free Survival Rates in Children Less Than 20 Years of Age in Acute Promyelocytic Leukemia (APL). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 957. http://www.bloodjournal.org/content/124/21/957.
  • Lew G, Lu X, Yanofsky R, Rheingold SR, Whitlock J, An Q, Devidas M, Hastings CA, Winick NJ, Carroll WL, Borowitz MJ, Hunger S, Pulsipher MA. Outcomes after Intermediate-Risk Relapse of Childhood B-Lymphoblastic Leukemia (B-ALL) and the Role of Allogeneic Stem Cell Transplantation (SCT): A Report from Children's Oncology Group (COG) AALL0433. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 684. http://www.bloodjournal.org/content/124/21/684.
  • Lew G, Lu X, Yanofsky RA, Rheingold SR, Whitlock JA, Gulig SD, Devidas M, Pulsipher MA, Hastings CA, Winick NJ, Carroll WL, Borowitz MJ, Hunger SP. The significance of minimal residual disease (MRD) in relapsed childhood B-lymphoblastic leukemia: Interim analysis of Children's Oncology Group (COG) protocol AALL0433. ASCO Annual Meeting. Chicago, IL; May 30-June 3, 2014. J Clin Oncol 32:5s(2014 suppl ); abstr 10014.
  • Majerus EM, Ataga KI, Vichinsky E, Eaton CA, Mazanet R, Nathan DG, Field JJ. NKTT120 Reduces iNKT Cells without Dose Limiting Toxicity in Stable Adult Sickle Cell Patients in a Phase 1 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2718. http://www.bloodjournal.org/content/124/21/2718.
  • Morris C, Latronica C, Kuypers FA, Rosenfeld H, Larkin SK, Doniger S, Vichinsky E, Shiva S. Citrate Synthase Activity Is Increased In Children With Sickle Cell Disease (SCD) On Hydroxyurea (HU) Therapy. 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL; April 2014.
  • Paulukonis S, Currier R, Coates TD, Vichinsky E, Feuchtbaum L. Impact of Immigration and Migration on Thalassemia Surveillance in California, 2004-2008. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4855-. http://www.bloodjournal.org/content/124/21/4855.
  • Paulukonis S, Griffin T, Zhou M, Eckman JR, Hagar R, Bauer Snyder A, Feuchtbaum L, Grant AM, Hulihan M. Sickle Cell Disease Mortality in California and Georgia 2004-2008. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 439-. http://www.bloodjournal.org/content/124/21/439.
  • Singer ST, Wang J, Yuan Q, Vichinsky E, Smith J, Paley C, Fischer R. Pituitary Iron and Volume Are Affecting Hormones and Reproductive Potential. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4048. https://ash.confex.com/ash/2014/webprogram/Paper75574.html.
  • Thompson AA, Rasko JE, Hongeng S, Kwiatkowski JL, Schiller G, von Kalle C, Cavazzana M, Leboulch P, Petrusich A, Soni S, Walters MC. Initial Results from the Northstar Study (HGB-204): A Phase 1/2 Study of Gene Therapy for ?-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral ??-T87Q -Globin Vector (LentiGlobin BB305 Drug Product). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 549. Nominated for Best of ASH abstract. http://www.bloodjournal.org/content/124/21/549.
  • Treadwell M, Paulukonis S, Currier B, Hutchinson C, Neumayr L, Vichinsky E, Feuchtbaum L. Population-based study of mental health diagnoses and utilization in sickle cell disease. Annual Sickle Cell Disease Research and Educational Symposium and 37th National Sickle Cell Disease Scientific Meeting. Miami, FL; April 11-14, 2014. Poster presentation.
  • Treadwell M, Johnson S, Sisler I, Gildengorin G, Medina R, Barreda F, Bitsko M, Smith WR. Evaluation of a sickle cell disease specific readiness for transition assessment. 8th Annual Sickle Cell Disease Research & Educational Symposium and 37th National Sickle Cell Disease Scientific Meeting. Miami, FL. April 11-14, 2014. Journal of Sickle Cell Disease and Hemoglobinopathies 2014(1; doi 10.14223/JSCDH-D-14-00081).
  • Vichinsky E, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, George A, Heeney MM. Clinical complications in pediatric and adult sickle cell disease. Association of Pediatric Hematology/Oncology Nurses (APHON) Annual Conference & Exhibit. Portland, OR; Sep 4-6 2014. poster presentation.
  • Walter PB, Hohman L, Rokeby A, Manocha A, Lum JJ, Lavrisha L, Stewart M, Hagar R, Vichinsky E, Morris CR. The effects of glutamine supplementation on markers of autophagy and apoptosis in peripheral blood mononuclear cells from patients with sickle cell disease. Free Radical Biology and Medicine. Seattle, WA; Nov 2014.
  • Walter PB, Hohman L, Rokeby A, Manocha A, Lum JJ, Lavrisha L, Stewart M, Hagar R, Vichinsky E, Morris CR. The effects of glutamine supplementation on markers of autophagy and apoptosis in peripheral blood mononuclear cells from patients with sickle cell disease. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).
  • Wun T, Telen MJ, Krishnamurti L, McCavit TL, DeCastro LM, Flanner H, Kuypers FA, Larkin SK, Rhee S, Magnani JL, Thackray HM. Pan-Selectin Antagonist Rivipansel (GMI-1070) Reduces Soluble E-Selectin Levels While Improving Clinical Outcomes in SCD Vaso-Occlusive Crisis. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2704. http://www.bloodjournal.org/content/124/21/2704.

The following sections are not yet complete and include only a small portion of our lectures, presentations and honors..


Awards and Honors:


Invited Lectures:

2015:

  • Hoppe C. Controversies in Managing Sickle Cell Disease: NCAA vs AAP vs NIH Recommendations. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.305-312. University of California, San Francisco, School of Medicine.
  • Lal A. Alpha Thalassemia Hb H Disease: An Emerging Public Health Problem. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.297-303. University of California, San Francisco, School of Medicine.
  • Matsunaga A. ITP Management Dilemmas. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.249-260. University of California, San Francisco, School of Medicine.
  • Treadwell M. Neurocognitive Issues in Sickle Cell Disease. West Coast Sickle Cell Nurses Annual Meeting; Sept 28, 2015, Los Angeles, CA.
  • Treadwell M. Person and Family Centered Outcomes. Clinical Data Research Network Annual Meeting; Mar 15-16, 2015; Vanderbilt Center of Excellence in Sickle Cell Disease, Nashville, TN.
  • Treadwell M. Quality of Life and Quality of Care in Adults with Sickle Cell Disease. 9th Annual Sickle Cell and Thalassaemia Advanced Conference; Oct 7-9, 2015; Guys & St. Thomas' NIH Foundation Trust, London, U.K.
  • Treadwell M. Sickle Cell Disease and Access to Care: a National Crisis. Annual Conference of the National Medical Association, Region IV; May 28, 2015.
  • Treadwell M. Sickle Cell Disease: Impact on Individuals and Families. Gene Editing and a Path to a Cure for Sickle Cell Disease; July 28, 2015; Congressional Briefing sponsored by the Sickle Cell Disease Association of America, the Congressional Sickle Cell Caucus and the Research and Development Caucus, Washington, D.C.
  • Treadwell M, Hodge J. Disparities in African American Health: Sickle Cell Disease. Mar 5, 2015; Office of Diversity and Inclusion, Samuel Merritt University, Oakland, CA.
  • Treadwell M, Murphy W, Johnson T, Lal A. Self-Efficacy and Adherence with Iron Chelation Therapies: Motivational Interviewing Interventions. Tenth Cooley's Anemia Symposium; Oct 18-22, 2015, Chicago, IL.
  • Treadwell M, Vichinsky E, Nugent D. Pacific Sickle Cell Regional Collaborative. Sickle Cell Disease Association of America 43rd Annual Convention; Sep 23-26, 2015, Baltimore, MD.
  • Vichinsky E. Iron Deficiency & Iron Metabolism Disorders: More Serious and Common Than You Think. Sello Ac, ed. 48th Annual Advances & Controversies in Clinical Pediatrics. San Francisco, CA; May 28-30, 2015; p.261-270. University of California, San Francisco, School of Medicine.
  • Vichinsky E. Diagnosis and Management of Iron Overload. ASH Consultative Hematology Course; Dec 7, 2015; American Society of Hematology, Orlando, FL; http://www.hematology.org/Annual-Meeting/Program/CHC.aspx.
  • Vichinsky E. Diagnosis and Management of Iron Overload. ASH Consultative Hematology Course; Sept 17, 2015; American Society of Hematology, Chicago, IL; http://www.hematology.org/Meetings/CHC/4010.aspx.

2014:

  • Lal A. Thalassemia Intermedia. UC Davis, Dept of Pediatrics, Grand Rounds; Feb 3, 2014; Davis, CA.
  • Lal A. Iron Chelation Therapy. Thalassemia Patient and Family Conference, Jan 18, 2014, UCSF Benioff Children's Hospital Oakland, Oakland, CA. http://www.thalassemia.com/2014-patient-family-conference.aspx.
  • Levine L. Progress. "Evening Under the Stars", May 3, 2014, Oakland CA. https://www.youtube.com/watch?v=UF5EeH01CNs.
  • Vichinsky E. The Complex Pathophysiology of the Hemoglobinopathies: Guiding Us to Innovative Challenges. Presidential Symposium; May 14-17, 2014, 27th Annual ASPHO Meeting, Chicago, IL.
  • Vichinsky E, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, George A, Heeney MM. Clinical complications in pediatric and adult sickle cell disease. Association of Pediatric Hematology/Oncology Nurses (APHON) Annual Conference & Exhibit. Portland, OR; Sep 4-6 2014. poster presentation.
  • Vichinsky E. Thalassemia Research and Care Update. Thalassemia Patient and Family Conference, Jan 18, 2014, Oakland CA.
  • Walters M. Bone Marrow/Stem Cell Transplant/Gene Therapy. Thalassemia Patient and Family Conference, Jan 18, 2014, Oakland CA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. May 4, 2014; Berkeley Stem Cell Center, Berkeley, CA.
  • Walters MC. Thalassemia Debate. European Hematology Association 19th Congress; June 10-15, 2014, Milan, Italy.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. July 29-30, 2014, Children's Hospital Los Angeles, CA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. Sep 5, 2014; Fred Hutchinson Cancer Research Center, Seattle, WA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. DeCal lecture; Sep 29, 2014; University of California, Berkeley, CA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. UCSF Hematology/Oncology Division; Oct 27, 2014; University of California, San Francisco, CA.
  • Walters MC. Bone marrow transplantation for hemoglobinopathies. UCSF/CHORI Translational Research Retreat; Oct 29, 2014; Oakland, CA.
  • Walters MC. Bone marrow transplantation and hematopoiesis. Nov 14, 2014; Bayer, San Francisco, CA.

Profiles:

updated 5 Jan 2016


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